- Pediatric Specialty CenterTrumbull Pediatric Specialty Center5520 Park Avenue, Ste 600Trumbull, CT 06611
- Smilow Cancer HospitalSmilow Cancer Hospital at Yale New Haven35 Park StreetNew Haven, CT 06511
- Pediatric Specialty CenterOld Saybrook Medical Center633 Middlesex Turnpike, Ste 110Old Saybrook, CT 06475
Michael Recht, MD, PhD, MBA
Biography
Michael Recht, MD, PhD, is a pediatric hematologist who focuses on treating children, adolescents, and young adults with bleeding and clotting disorders.
Dr. Recht is a professor of clinical pediatrics at Yale School of Medicine. He has been actively involved in more than 110 clinical trials, including research on gene therapy for hemophilia. Dr. Recht also serves as the chief medical and scientific officer for the National Bleeding Disorders Foundation. In this role, he helps shape the scientific direction and research strategy of the organization, working to advance the understanding and treatment of bleeding disorders. Dr. Recht received his medical and doctoral degrees from the University of Wisconsin-Madison. He completed his residency in pediatrics and fellowship in pediatric hematology-oncology at Yale New Haven Hospital.
Titles
- Professor of Clinical Pediatrics (Hematology/Oncology)
- Chief Medical and Scientific Officer, National Hemophilia Foundation, National Hemophilia Foundation
Education & Training
- MBAOregon Health & Science University/Portland State University (2016)
- FellowYale University School of Medicine (1998)
- ResidentYale New Haven Hospital (1995)
- MDUniversity of Wisconsin-Madison (1992)
- PhDUniversity of Wisconsin-Madison (1990)
Additional Information
- Chrisentery-Singleton T, Acharya S, Ahuja S, Amos L, Chitlur M, Daoud N, Eason A, Escobar M, Fedor C, Gupta S, Kuriakose P, Nasr S, Pennington S, Pruthi R, Recht M, Robertson A, Quon D, Wheeler A, Reding M. Safety and real-world effectiveness of eptacog beta with emicizumab prophylaxis: an interim analysis of the ATHN 16 study. Blood Vessels Thrombosis & Hemostasis 2026, 3: 100169. DOI: 10.1016/j.bvth.2026.100169.
- Czura C, Weyand A, Baldwin M, Recht M, Benner C, Harada K, Wade B, Luellen M, Darrow M, McWade M, Covalin A, Khodaparast N. A novel transcutaneous auricular neurostimulation electrode configuration for treatment of heavy menstrual bleeding: an open-label trial. Bioelectronic Medicine 2026, 12: 10. PMID: 41933398, PMCID: PMC13049727, DOI: 10.1186/s42234-026-00203-1.
- Pipe S, Miesbach W, Recht M, Leebeek F, Key N, Castaman G, Lattimore S, Coppens M, Le Quellec S, Mahajan V, Gill S, Drelich D, Monahan P. Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia B. The New England Journal Of Medicine 2025, 394: 463-474. PMID: 41358585, DOI: 10.1056/nejmoa2514332.
- Buckner T, Carpenter S, Daoud N, Kempton C, Lee L, Malec L, McLean T, Morton P, O'Neill C, Staber J, Wang M, Croteau S, Recht M. Safety and Effectiveness of Emicizumab in People With Haemophilia A Enrolled in the ATHN 7 Haemophilia Natural History Study. Haemophilia 2025, 32: 63-70. PMID: 41220279, PMCID: PMC12904170, DOI: 10.1111/hae.70151.
- Czura C, Weyand A, Baldwin M, Recht M, McWade M, Covalin A, Khodaparast N. Transcutaneous auricular neurostimulation to reduce heavy menstrual bleeding in women with and without von Willebrand disease. Frontiers In Medicine 2025, 12: 1664433. PMID: 41133152, PMCID: PMC12540315, DOI: 10.3389/fmed.2025.1664433.
- Klamroth R, Recht M, Key N, Miesbach W, Pipe S, Kaczmarek R, Drelich D, Salazar B, Le Quellec S, Monahan P, Galante N, van der Valk P, Tarrant J. Natural history of preexisting AAV5 antibodies in adults with hemophilia B during the lead-in of the etranacogene dezaparvovec phase 3 study. Molecular Therapy Advances 2025, 33: 101568. PMID: 40969675, PMCID: PMC12441693, DOI: 10.1016/j.omtm.2025.101568.
- Chandler M, Moulton T, Charafi L, Charlet J, Recht M. Effectiveness of Octocog Alfa (BAY 81‐8973) to Treat People With Haemophilia A Enrolled in the ATHNdataset, Including Under‐Represented Subgroups. European Journal Of Haematology 2025, 115: 484-492. PMID: 40770897, PMCID: PMC12505839, DOI: 10.1111/ejh.70016.
- Valentino L, Santaella M, Witkop M, Stanhope R, Valadez S, Carlson S, Benasutti H, DiMichele D, Recht M. The Bleeding Disorders Research Collaborative. Blood Vessels Thrombosis & Hemostasis 2025, 2: 100099. PMID: 41070002, PMCID: PMC12506547, DOI: 10.1016/j.bvth.2025.100099.
- von Drygalski A, Gomez E, Giermasz A, Castaman G, Key N, Lattimore S, Leebeek F, Miesbach W, Recht M, Monahan P, Le Quellec S, Pipe S. Completion of phase 2b trial of etranacogene dezaparvovec gene therapy in patients with hemophilia B over 5 years. Blood Advances 2025, 9: 3543-3552. PMID: 40188458, PMCID: PMC12275190, DOI: 10.1182/bloodadvances.2024015291.
- Madan B, Ozelo M, Kenet G, Chou S, Dashiell-Aje E, Robinson T, Mahlangu J, Recht M, Careta F, Ruiz A, Fletcher S, Goshen D. Plain language summary of 4-year results of the GENEr8-1 clinical trial of valoctocogene roxaparvovec gene therapy for hemophilia A. Future Rare Diseases 2025, 5: 2522071. DOI: 10.1080/23995270.2025.2522071.
- Buckner T, Kessler C, Castaman G, Hermans C, Jiménez‐Yuste V, Mahlangu J, Miesbach W, Oldenburg J, Recht M, Valentino L, Wheeler A, Pipe S. Pain Reduction Following Eptacog Beta Treatment of Bleeding Episodes in Adolescents and Adults With Haemophilia A or B Complicated by Inhibitors. Haemophilia 2025, 31: 713-721. PMID: 40534395, DOI: 10.1111/hae.70077.
- Thornburg C, van den Berg H, Chandler M, Malec L, Manuel M, O’Neill C, Recht M, Taggart E, Carpenter S, group A, Knoll C, Malec L, Wang M, Guerrera M, Tarango C, Sidonio R, Rodriguez N, Friedman K, Shapiro A, Yaish H, Carpenter S, Janbain M, Grabowski E, Pruthi R, Haley K, Thornburg C, Ahuja S, Simpson M, Reiss U, Lucas T, Balasa V, Wheeler A. Inhibitor development and clinical characteristics in children with severe hemophilia A in the ATHN 8 US cohort study. Blood Vessels Thrombosis & Hemostasis 2025, 2: 100082. PMID: 40918739, PMCID: PMC12412393, DOI: 10.1016/j.bvth.2025.100082.
- Konkle B, Peyvandi F, Foster G, Hermans C, La Mura V, Leavitt A, Lillicrap D, Mahlangu J, Ozelo M, Pipe S, Recht M, Srivastava A, Young G, Miesbach W. Corticosteroid use to mitigate transaminitis-associated decline in FVIII levels following valoctocogene roxaparvovec gene therapy: clinical practice guidance. Journal Of Thrombosis And Haemostasis 2025, 23: 2086-2094. PMID: 40090623, DOI: 10.1016/j.jtha.2025.02.042.
- Chrisentery‐Singleton T, Gattone P, Gerber C, Mills K, Miles M, Rotellini D, Santaella M, Valentino L, Watson C, Recht M. American Thrombosis and Hemostasis Network: National Bleeding Disorders Foundation Data Commons: Better Together. Haemophilia 2025, 31: 589-593. PMID: 39982786, DOI: 10.1111/hae.70011.
- Valentino L, Santaella M, Carlson S, Recht M. Contemporary approaches to treat people with hemophilia: what’s new and what’s not? Research And Practice In Thrombosis And Haemostasis 2025, 9: 102696. PMID: 40084158, PMCID: PMC11905833, DOI: 10.1016/j.rpth.2025.102696.
- Dunn A, Dargaud Y, Abajas Y, Carcao M, Castaman G, Giermasz A, Hermans C, Jiménez‐Yuste V, Lewandowska M, Mahlangu J, Meeks S, Miesbach W, Recht M, Salinas V, Chrisentery‐Singleton T, Bonzo D, Mitchell I, Wilkinson T, Young G. Bleed treatment with eptacog beta (rFVIIa) results in a low incidence of rebleeding in adult and adolescent patients with haemophilia A or B with inhibitors. Haemophilia 2024, 31: 78-86. PMID: 39676340, PMCID: PMC11780187, DOI: 10.1111/hae.15109.
- Skinner M, Albisetti M, Ardila J, Astermark J, Blatny J, Carcao M, Chowdary P, Connell N, Crato M, Dargaud Y, d'Oiron R, Dunn A, Escobar M, Escuriola‐Ettingshausen C, Gouider E, Harroche A, Hermans C, Jimenez‐Yuste V, Kaczmarek R, Kenet G, Khoo L, Klamroth R, Langer F, Lillicrap D, Mahlangu J, Male C, Matsushita T, Meunier S, Miesbach W, Nolan B, Oldenburg J, O'Mahony B, Ozelo M, Pierce G, Ramos G, Recht M, Romero‐Lux O, Rotellini D, Santoro R, Singleton T, Srivastava A, Susen S, Talks K, Tran H, Valentino L, Windyga J, Yang R, Mancuso M, also on behalf of AICE A. Contrasting Approaches in the Implementation of GRADE Methodology in Guidelines for Haemophilia and Von Willebrand Disease. Haemophilia 2024 PMID: 39648854, DOI: 10.1111/hae.15136.
- Albisetti M, Ardila J, Astermark J, Blatny J, Carcao M, Chowdary P, Connell N, Crato M, Dargaud Y, d'Oiron R, Dunn A, Escobar M, Ettingshausen C, Fischer K, Gouider E, Harroche A, Hermans C, Jimenez‐Yuste V, Kaczmarek R, Kenet G, Khoo L, Klamroth R, Langer F, Lillicrap D, Mahlangu J, Male C, Mancuso M, Matsushita T, Meunier S, Miesbach W, Nolan B, Oldenburg J, O'Mahony B, Ozelo M, Pierce G, Ramos G, Recht M, Romero‐Lux O, Rotellini D, Santoro R, Singleton T, Skinner M, Srivastava A, Susen S, Talks K, Tran H, Valentino L, Windyga J, Yang R, also on behalf of AICE A. International Society on Thrombosis and Haemostasis Clinical Practice Guideline for Treatment of Congenital Haemophilia—A Critical Appraisal. Haemophilia 2024 PMID: 39642092, DOI: 10.1111/hae.15135.
- Chandler M, Moulton T, Charafi L, Charlet J, Recht M. Effectiveness of Damoctocog Alfa Pegol to Treat Patients With Hemophilia A Enrolled in the ATHNdataset. European Journal Of Haematology 2024, 114: 448-457. PMID: 39558414, PMCID: PMC11798759, DOI: 10.1111/ejh.14337.
- Youkhana K, Batsuli G, Acharya S, Khan O, Tran D, Dvorak A, Recht M, Young G, Sidonio R, Abajas Y. Real‐world effectiveness of eptacog beta in patients with haemophilia and inhibitors: A multi‐institutional case series. Haemophilia 2024, 30: 1321-1331. PMID: 39297369, PMCID: PMC11659498, DOI: 10.1111/hae.15094.
- DeSancho M, Suvar E, Roberts J, Tarantino M, Schwartz J, Callis J, Recht M. Hereditary antithrombin deficiency pilot project registry from the American Thrombosis and Hemostasis Network. Journal Of Thrombosis And Haemostasis 2024, 22: 3183-3190. PMID: 39151704, DOI: 10.1016/j.jtha.2024.07.026.
- Pierce G, O'Mahony B, Kaczmarek R, Skinner M, Makris M, Peyvandi F, Srivastava A, Hermans C, World Federation of Hemophilia Coagulation Products Supply S, Crato M, Dunn A, Gouider E, Mahlangu J, Page D, Pipe S, Recht M, Sannie T, Schaefer N, Schlenkrich U, Garrido C. Risk of harm to people with haemophilia from the 2023 WHO Essential Medicines List. The Lancet Haematology 2024, 11: e638-e640. PMID: 39116903, DOI: 10.1016/s2352-3026(24)00223-0.
- Nolan B, Recht M, Rendo P, Falk A, Foster M, Casiano S, Rauch A, Shapiro A. Prophylaxis with recombinant factor IX Fc fusion protein reduces the risk of bleeding and delays time to first spontaneous bleed event in previously untreated patients with haemophilia B: A post hoc analysis of the PUPs B‐LONG study. European Journal Of Haematology 2024, 113: 485-492. PMID: 38922990, DOI: 10.1111/ejh.14252.
- Hu J, Chandler M, Manuel C, Caicedo J, Denne M, Ewenstein B, Mokdad A, Xing S, Recht M. Risk of Intracranial Hemorrhage in Persons with Hemophilia A in the United States: Real-World Retrospective Cohort Study Using the ATHNdataset. Journal Of Blood Medicine 2024, 15: 191-205. PMID: 38699197, PMCID: PMC11063465, DOI: 10.2147/jbm.s443380.
- Itzler R, Buckner T, Leebeek F, Miller J, Recht M, Drelich D, Monahan P, Pipe S. Effect of etranacogene dezaparvovec on quality of life for severe and moderately severe haemophilia B participants: Results from the phase III HOPE‐B trial 2 years after gene therapy. Haemophilia 2024, 30: 709-719. PMID: 38462823, DOI: 10.1111/hae.14977.
- Coppens M, Pipe S, Miesbach W, Astermark J, Recht M, van der Valk P, Ewenstein B, Pinachyan K, Galante N, Le Quellec S, Monahan P, Leebeek F, Investigators H, Castaman G, Crary S, Escobar M, Gomez E, Haley K, Hermans C, Kampmann P, Kazmi R, Key N, Klamroth R, Konkle B, Kruse-Jarres R, Lattimore S, Lemons R, Meijer K, O'Connell N, Quon D, Raheja P, Symington E, Verhamme P, Visweshwar N, von Drygalski A, Wang M, Wheeler A, White S, Young G. Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial. The Lancet Haematology 2024, 11: e265-e275. PMID: 38437857, DOI: 10.1016/s2352-3026(24)00006-1.
- Ragni M, Callis J, Daoud N, Hu B, Manuel M, Santos J, Schwartz J, Friedman K, Kouides P, Kuriakose P, Leavitt A, Lim M, Machin N, Recht M, Chrisentery‐Singleton T. Observational cohort study of long‐term outcomes of liver transplantation in haemophilia. Haemophilia 2023, 30: 87-97. PMID: 38111071, DOI: 10.1111/hae.14910.
- von Drygalski A, Gomez E, Giermasz A, Castaman G, Key N, Lattimore S, Leebeek F, Miesbach W, Recht M, Gut R, Dolmetsch R, Monahan P, Le Quellec S, Pipe S. Stable and durable factor IX levels in hemophilia B patients over 3 years post etranacogene dezaparvovec gene therapy. Blood Advances 2023, 7: 5671-5679. PMID: 36490302, PMCID: PMC10539871, DOI: 10.1182/bloodadvances.2022008886.
- Valentino L, Witkop M, Santaella M, DiMichele D, Recht M. The National Hemophilia Foundation State of the Science Research Summit initiative: executive summary. Expert Review Of Hematology 2023, 16: 129-134. PMID: 36920857, DOI: 10.1080/17474086.2023.2181782.
- Valentino L, Witkop M, Santaella M, DiMichele D, Recht M. The National Hemophilia Foundation’s State of the Science Research Summit: the foundation of a national research blueprint for inherited bleeding disorders. Expert Review Of Hematology 2023, 16: 1-5. PMID: 36920858, DOI: 10.1080/17474086.2023.2178412.
- Nugent D, Acharya S, Baumann K, Bedrosian C, Bialas R, Brown K, Corzo D, Haidar A, Hayward C, Marks P, Menegatti M, Miller M, Nammacher K, Palla R, Peltier S, Pruthi R, Recht M, Sørensen B, Tarantino M, Wolberg A, Shapiro A. Building the foundation for a community-generated national research blueprint for inherited bleeding disorders: research priorities for ultra-rare inherited bleeding disorders. Expert Review Of Hematology 2023, 16: 55-70. PMID: 36920862, PMCID: PMC10020868, DOI: 10.1080/17474086.2023.2175661.
- Messenger H, Kulkarni R, Recht M, He C. A Retrospective Analysis of the American Thrombosis and Hemostasis Network Dataset Describing Outcomes of Dental Extractions in Persons with Hemophilia. Journal Of Clinical Medicine 2023, 12: 1839. PMID: 36902626, PMCID: PMC10002874, DOI: 10.3390/jcm12051839.
- Van der Valk P, Pipe S, Key N, Castaman G, Kampmann P, O’Connell N, Hart D, Kazmi R, Astermark J, Klamroth R, Lemons R, Visweshwar N, von Drygalski A, Young G, Escobar M, Gomez E, Symington E, Wang M, Wheeler A, Gut R, Cooper D, Li Y, Goldstein B, Monahan P, Leebeek F, Hermans C, Dolmetsch R, Lattimore S, Peerlinck K, Meijer K, Crary S, Kruse-Jarres R, Quon D, Liu Y, Recht M, Miesbach W, Coppens M, Pasi K. Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B. The New England Journal Of Medicine 2023, 388: 706-718. PMID: 36812434, DOI: 10.1056/nejmoa2211644.
- Parker K, Durben N, Oleson D, Yu Y, Lim J, Recht M, Lindemulder S. Hopping as an Indicator of Chemotoxicity: Gait Analysis in Patients With Leukemia and Lymphoma. Journal Of Pediatric Hematology/Oncology 2023, 45: e582-e589. PMID: 36898017, DOI: 10.1097/mph.0000000000002645.
- Corrales-Medina F, Raffini L, Recht M, Santos J, Thornburg C, Davila J, Investigators A. Direct oral anticoagulants in pediatric venous thromboembolism: Experience in specialized pediatric hemostasis centers in the United States. Research And Practice In Thrombosis And Haemostasis 2022, 7: 100001. PMID: 36970740, PMCID: PMC10031368, DOI: 10.1016/j.rpth.2022.100001.
- Johnsen J, Fletcher S, Dove A, McCracken H, Martin B, Kircher M, Josephson N, Shendure J, Ruuska S, Valentino L, Pierce G, Watson C, Cheng D, Recht M, Konkle B. Results of genetic analysis of 11 341 participants enrolled in the My Life, Our Future hemophilia genotyping initiative in the United States. Journal Of Thrombosis And Haemostasis 2022, 20: 2022-2034. PMID: 35770352, DOI: 10.1111/jth.15805.
- Roberts J, Richardson S, Miles M, Stanley J, Chapman C, Denne M, Caicedo J, Rockwood K, Recht M. The GOAL‐Hēm journey: Shared decision making and patient‐centred outcomes. Haemophilia 2022, 28: 784-795. PMID: 35728103, PMCID: PMC9546188, DOI: 10.1111/hae.14608.
- Valentino L, Witkop M, Santaella M, DiMichele D, Recht M. Building the blueprint: Formulating a community‐generated national plan for future research in inherited bleeding disorders. Haemophilia 2022, 28: 760-768. PMID: 35700441, PMCID: PMC9546016, DOI: 10.1111/hae.14588.
- Rauch A, Valentino L, Mills K, Witkop M, Santaella M, DiMichele D, Recht M, Susen S. Big picture initiatives in bleeding disorders. Haemophilia 2022, 28: 53-60. PMID: 35521733, DOI: 10.1111/hae.14532.
- Pipe S, Hermans C, Chitlur M, Carcao M, Castaman G, Davis J, Ducore J, Dunn A, Escobar M, Journeycake J, Khan O, Mahlangu J, Meeks S, Mitha I, Négrier C, Nowak‐Göttl U, Recht M, Chrisentery‐Singleton T, Stasyshyn O, Vilchevska K, Martinez L, Wang M, Windyga J, Young G, Alexander W, Bonzo D, Macie C, Mitchell I, Sauty E, Wilkinson T, Shapiro A. Eptacog beta efficacy and safety in the treatment and control of bleeding in paediatric subjects (<12 years) with haemophilia A or B with inhibitors. Haemophilia 2022, 28: 548-556. PMID: 35475308, PMCID: PMC9542908, DOI: 10.1111/hae.14563.
- Recht M, He C, Chen E, Cheng D, Solari P, Hinds D. Resource utilization and treatment costs of patients with severe hemophilia A: Real‐world data from the ATHNdataset. EJHaem 2022, 3: 341-352. PMID: 35846041, PMCID: PMC9176109, DOI: 10.1002/jha2.412.
- Burke T, Shaikh A, Ali T, Li N, Curtis R, Diego D, Recht M, Sannie T, Skinner M, O’Hara J. Association of factor expression levels with health-related quality of life and direct medical costs for people with haemophilia B. Journal Of Medical Economics 2022, 25: 386-392. PMID: 35253589, DOI: 10.1080/13696998.2022.2049552.
- Goldenberg N, Kittelson J, Abshire T, Bonaca M, Casella J, Dale R, Halperin J, Hamblin F, Kessler C, Manco-Johnson M, Sidonio R, Spyropoulos A, Steg P, Turpie A, Schulman S, French J, Fargo J, Crary S, Kumar R, Grace R, Trenor C, Wilson H, Hilliard L, Woods G, Patel K, Goldenberg N, Lowe E, Jaffray J, Young G, Rajpurkar M, Davila J, Mahajerin A, Cooper J, Gunawardena S, Zia A, Journeycake J, Carpenter S, Guerrera M, Diab Y, Tarango C, Gruppo R, Acharya S, Torres M, Shaffer L, Mignacca R, Haley K, Recht M, Thornburg C, Shah N, Mullen C, Mitchell D, Nakar C, Betensky M, Lawrence C, Takemoto C, Lo C, Scott-Emuakpor A, Kulkarni R, Borst A, O'Brien S, Corales-Medina F, Narang S, Kucine N, Wang M, Panigrahi A, McGowan K, Cramer S, Dandekar S, Xavier F, Knoll K, Verma A, Geddes A, Ahuja S, Hege K, Raybagkar D, Sharathkumar A, Srivath L, Khan O, Druzgal C, Bhatt M, Chan A, Brandao L, Massicotte P, van Ommen C, Male C, Monagle P, Nakano T, Mitchell W, Hiatt W, Weitz J. Effect of Anticoagulant Therapy for 6 Weeks vs 3 Months on Recurrence and Bleeding Events in Patients Younger Than 21 Years of Age With Provoked Venous Thromboembolism. JAMA: The Journal Of The American Medical Association 2022, 327: 129-137. PMID: 35015038, PMCID: PMC8753509, DOI: 10.1001/jama.2021.23182.
- Roberts J, Recht M, Gonzales S, Stanley J, Denne M, Caicedo J, Rockwood K. Incorporating the patient voice and patient engagement in GOAL‐Hēm: Advancing patient‐centric hemophilia care. Research And Practice In Thrombosis And Haemostasis 2022, 6: e12655. PMID: 35155975, PMCID: PMC8822263, DOI: 10.1002/rth2.12655.
- Buckner T, Daoud N, Miles M, O'Neill C, Watson C, Recht M. Designing ATHN 7: Safety, effectiveness and practice of treatment of people with haemophilia in the United States through a natural history cohort study. The Journal Of Haemophilia Practice 2022, 9: 147-155. DOI: 10.2478/jhp-2022-0020.
- Eyster M, Sullivan S, MacDougall A, Jaworski K, Noble R, Curran M, Kuranda K, Chang T, Reape K, George L, Monahan P, Ragni M, Croteau S, Rasko J, Recht M, Samelson-Jones B, Mingozzi F, Anguela X, High K. Multiyear Factor VIII Expression after AAV Gene Transfer for Hemophilia A. The New England Journal Of Medicine 2021, 385: 1961-1973. PMID: 34788507, PMCID: PMC8672712, DOI: 10.1056/nejmoa2104205.
- He C, Hinds D, Pezalla E, Cheng D, Chen E, Sammon J, Solari P, Recht M. Health insurance coverage and switching among people with hemophilia A in the United States. Journal Of Managed Care & Specialty Pharmacy 2021, 28: 232-243. PMID: 34780299, PMCID: PMC12128936, DOI: 10.18553/jmcp.2021.21311.
- Valentino L, Baker J, Butler R, Escobar M, Frick N, Karp S, Koulianos K, Lattimore S, Nugent D, Pugliese J, Recht M, Reding M, Rice M, Thibodeaux C, Skinner M. Integrated Hemophilia Patient Care via a National Network of Care Centers in the United States: A Model for Rare Coagulation Disorders. Journal Of Blood Medicine 2021, 12: 897-911. PMID: 34707421, PMCID: PMC8544265, DOI: 10.2147/jbm.s325031.
- Veeranki S, Pednekar P, Graf M, Tuly R, Recht M, Batt K. A Delphi Consensus Approach for Difficult-to-Treat Patients with Severe Hemophilia A without Inhibitors. Journal Of Blood Medicine 2021, 12: 913-928. PMID: 34707422, PMCID: PMC8544791, DOI: 10.2147/jbm.s334852.
- Konkle B, Quon D, Raffini L, Recht M, Radulescu V, Carpenter S, Dunn A, Lu M, Watt M. A Prospective Observational Study of Antihemophilic Factor (Recombinant) Prophylaxis Related to Physical Activity Levels in Patients with Hemophilia A in the United States (SPACE). Journal Of Blood Medicine 2021, 12: 883-896. PMID: 34703348, PMCID: PMC8523903, DOI: 10.2147/jbm.s327180.
- Escobar M, Castaman G, Boix S, Callaghan M, de Moerloose P, Ducore J, Hermans C, Journeycake J, Leissinger C, Luck J, Mahlangu J, Miesbach W, Mitha I, Négrier C, Quon D, Recht M, Schved J, Shapiro A, Sidonio R, Srivastava A, Stasyshyn O, Vilchevska K, Wang M, Young G, Alexander W, Al‐Sabbagh A, Bonzo D, Macie C, Wilkinson T, Kessler C. The safety of activated eptacog beta in the management of bleeding episodes and perioperative haemostasis in adult and paediatric haemophilia patients with inhibitors. Haemophilia 2021, 27: 921-931. PMID: 34636112, PMCID: PMC9292935, DOI: 10.1111/hae.14419.
- Garrison L, Pezalla E, Towse A, Yang H, Faust E, Wu E, Li N, Sawyer E, Recht M. Hemophilia Gene Therapy Value Assessment: Methodological Challenges and Recommendations. Value In Health 2021, 24: 1628-1633. PMID: 34711363, DOI: 10.1016/j.jval.2021.05.008.
- Witkop M, Morgan G, O'Hara J, Recht M, Buckner T, Nugent D, Curtis R, O'Mahony B, Skinner M, Mulhern B, Cawson M, Ali T, Sawyer E, Li N. Patient preferences and priorities for haemophilia gene therapy in the US: A discrete choice experiment. Haemophilia 2021, 27: 769-782. PMID: 34310811, PMCID: PMC9290457, DOI: 10.1111/hae.14383.
- Nolan B, Klukowska A, Shapiro A, Rauch A, Recht M, Ragni M, Curtin J, Gunawardena S, Mukhopadhyay S, Jayawardene D, Winding B, Fischer K, Liesner R. Final results of the PUPs B-LONG study: evaluating safety and efficacy of rFIXFc in previously untreated patients with hemophilia B. Blood Advances 2021, 5: 2732-2739. PMID: 34242387, PMCID: PMC8288672, DOI: 10.1182/bloodadvances.2020004085.
- Sampson M, Cheng D, Recht M, Fargo J. The effect of age at diagnosis of type 1 von Willebrand disease on diagnostic laboratory values: A paediatric perspective. Haemophilia 2021, 27: e412-e414. PMID: 33533138, DOI: 10.1111/hae.14265.
- Recht M. Safety first: Tracking adverse events associated with new therapies for people with hemophilia. Journal Of Thrombosis And Haemostasis 2021, 19: 3-5. PMID: 33331044, DOI: 10.1111/jth.15188.
- Witkop M, Wang M, Hernandez G, Recht M, Baumann K, Cooper D. Impact of haemophilia on patients with mild‐to‐moderate disease: Results from the P‐FiQ and B‐HERO‐S studies. Haemophilia 2021, 27: 8-16. PMID: 33522654, DOI: 10.1111/hae.14251.
- Li N, Sawyer E, Maruszczyk K, Guzauskas G, Slomka M, Burke T, Martin A, O’Hara J, Stevenson M, Recht M. Adult lifetime cost of hemophilia B management in the US: payer and societal perspectives from a decision analytic model. Journal Of Medical Economics 2021, 24: 363-372. PMID: 33591884, DOI: 10.1080/13696998.2021.1891088.
- Reipert B, Gangadharan B, Hofbauer C, Berg V, Schweiger H, Bowen J, Blatny J, Fijnvandraat K, Mullins E, Klintman J, Male C, McGuinn C, Meeks S, Radulescu V, Ragni M, Recht M, Shapiro A, Staber J, Yaish H, Santagostino E, Brown D. The prospective Hemophilia Inhibitor PUP Study reveals distinct antibody signatures prior to FVIII inhibitor development. Blood Advances 2020, 4: 5785-5796. PMID: 33232473, PMCID: PMC7686884, DOI: 10.1182/bloodadvances.2020002731.
- Lim M, Cheng D, Recht M, Kempton C, Key N. Management of inhibitors in persons with non‐severe hemophilia A in the United States. American Journal Of Hematology 2020, 96: e9-e11. PMID: 32976635, DOI: 10.1002/ajh.26011.
- Lim M, Cheng D, Recht M, Kempton C, Key N. Inhibitors and mortality in persons with nonsevere hemophilia A in the United States. Blood Advances 2020, 4: 4739-4747. PMID: 33007074, PMCID: PMC7556148, DOI: 10.1182/bloodadvances.2020002626.
- Goldscheitter G, Recht M, Sochacki P, Manco‐Johnson M, Taylor J. Biomarkers of bone disease in persons with haemophilia. Haemophilia 2020, 27: 149-155. PMID: 32856388, DOI: 10.1111/hae.13986.
- Ahuja S, Recht M, Konkle B. Hemostatic Therapies for Heavy Menstrual Bleeding. 2020, 119-127. DOI: 10.1007/978-3-030-48446-0_11.
- Malec L, Cheng D, Witmer C, Jaffray J, Kouides P, Haley K, Sidonio R, Johnson K, Recht M, White G, Croteau S, Ragni M. The impact of extended half‐life factor concentrates on prophylaxis for severe hemophilia in the United States. American Journal Of Hematology 2020, 95: 960-965. PMID: 32356313, DOI: 10.1002/ajh.25844.
- Wang M, Recht M, Iyer N, Cooper D, Soucie J. Hemophilia without prophylaxis: Assessment of joint range of motion and factor activity. Research And Practice In Thrombosis And Haemostasis 2020, 4: e12347. PMID: 32864554, PMCID: PMC7443428, DOI: 10.1002/rth2.12347.
- Marshall A, Recht M, Sridharan M, Nichols W, Ashrani A, Fischer K, Miles M, Riedel A, Pruthi R. A study of dedicated haemophilia carrier clinics in the United States: Prevalence, services offered and barriers to development. Haemophilia 2020, 26: e253-e255. PMID: 32537802, DOI: 10.1111/hae.14071.
- Konkle B, Recht M, Hilger A, Marks P. The critical need for postmarketing surveillance in gene therapy for haemophilia. Haemophilia 2020, 27: 126-131. PMID: 32495492, DOI: 10.1111/hae.13972.
- Warren B, Thornhill D, Stein J, Fadell M, Ingram J, Funk S, Norton K, Lane H, Bennett C, Dunn A, Recht M, Shapiro A, Manco-Johnson M. Young adult outcomes of childhood prophylaxis for severe hemophilia A: results of the Joint Outcome Continuation Study. Blood Advances 2020, 4: 2451-2459. PMID: 32492157, PMCID: PMC7284094, DOI: 10.1182/bloodadvances.2019001311.
- Buckner T, Watson C, Recht M. Emicizumab in Hemophilia A. The New England Journal Of Medicine 2020, 382: 785-786. PMID: 32074441, DOI: 10.1056/nejmc1916299.
- Haley K, Sidonio R, Abraham S, Cheng D, Recht M, Kulkarni R. A Cross-Sectional Study of Women and Girls with Congenital Bleeding Disorders: The American Thrombosis and Hemostasis Network Cohort. Journal Of Women's Health 2020, 29: 670-676. PMID: 31905045, DOI: 10.1089/jwh.2019.7930.
- Von Drygalski A, Giermasz A, Castaman G, Key N, Lattimore S, Leebeek F, Miesbach W, Recht M, Long A, Gut R, Sawyer E, Pipe S. Etranacogene dezaparvovec (AMT-061 phase 2b): normal/near normal FIX activity and bleed cessation in hemophilia B. Blood Advances 2019, 3: 3241-3247. PMID: 31698454, PMCID: PMC6855101, DOI: 10.1182/bloodadvances.2019000811.
- Konkle B, Recht M, Group T. The national blueprint for 21st century data and specimen collection and observational cohort studies: NHLBI State of the Science Workshop on factor VIII inhibitors. Haemophilia 2019, 25: 590-594. PMID: 31329362, DOI: 10.1111/hae.13772.
- Warren B, Jacobson L, Kempton C, Buchanan G, Recht M, Brown D, Leissinger C, Shapiro A, Abshire T, Manco-Johnson M, Manco-Johnson M, Abshire T, Shapiro A, Riske B, Hacker M, Kilcoyne R, Ingram J, Manco-Johnson M, Funk S, Jacobson L, Valentino L, Hoots W, Buchanan G, DiMichele D, Recht M, Brown D, Leissinger C, Bleak S, Cohen A, Mathew P, Matsunaga A, Medeiros D, Nugent D, Thomas G, Thompson A, McRedmond K, Soucie J, Austin H, Evatt B. Factor VIII prophylaxis effects outweigh other hemostasis contributors in predicting severe haemophilia A joint outcomes. Haemophilia 2019, 25: 867-875. PMID: 31115111, PMCID: PMC7273872, DOI: 10.1111/hae.13778.
- Yu J, Iorio A, Edginton A, co‐investigators O, Ahuja S, Román M, Arrieta M, Arola M, Barillari G, Balasa V, Belletrutti M, Moreno R, Beurrier P, Bidlingmaier C, Blanchette V, Blatny J, Bonanad S, Brose K, Brown D, Byant P, Canaro M, Carvalho M, Catarino C, Chitlur M, Cockrell E, Chowdary P, Cnossen M, Collins P, Coppens M, Croteau S, Cultrera D, de Cristofaro R, de Raucourt E, Desprez D, Dunn A, El‐Ekiabi M, Kotnik B, Fischer K, Frotscher B, Garbiero S, Ruiz R, Gill J, del Castillo C, Gottstein S, Lassandro G, Giordano P, Hart D, Hegemann I, Hermans C, Hua B, Hwang N, Jackson S, James P, Katsarou O, Kavakli K, Kempton C, Kentouche K, Khan O, Kobelt R, Kruse‐Jarres R, Laane E, Larson E, Lassila R, Lee A, Poon M, Lissick J, Langstrom S, Mahlangu J, Makris M, Marchesini E, Mateo J, Vera P, Martorell M, Matsushita T, McCrae S, Mignot‐Castellano E, Montcrieff C, Maes P, Mondelars V, Bekart M, Mora E, Morales J, Mourey G, Bertrand M, Napolitano M, Siragusa S, Negrier C, Neme D, Niinimaki R, Oldenburg J, Albert T, Ornstein D, Ozelo M, Panetta J, Neufeld E, P'Ng S, Peerlinck K, Pollio B, Pouplard C, Gruel Y, Prezotti A, Price V, Primacakti F, Puyade M, Radossi P, Raffini L, Ragni M, Rangarajan S, Reding M, Reid R, Restrepo J, Ramirez J, Recht M, Lopez M, Ruiz‐Sàez A, Saleh M, Shapiro A, Sharathkumar A, Selmeczi A, Simpson M, Singleton T, Cruz M, Soto V, Steele M, Streif W, Sun H, Ritchie B, Sun J, Feng X, Suzuki T, Nagao A, Takemoto C, Tapp H, Teitel J, Tinmouth A, Thornburg C, Tosseto A, Turnstall O, Vezina C, Warren B, Wheeler A, Gutierrez J, Wu J, Wynn T, Yang R, Young G, Zanon E, Zupan I. Using pharmacokinetics for tailoring prophylaxis in people with hemophilia switching between clotting factor products: A scoping review. Research And Practice In Thrombosis And Haemostasis 2019, 3: e12204. PMID: 31294337, PMCID: PMC6611373, DOI: 10.1002/rth2.12204.
- Mahlangu J, Oldenburg J, Callaghan M, Shima M, Mancuso M, Trask P, Recht M, Garcia C, Yang R, Lehle M, Macharia H, Asikanius E, Levy G, Kruse‐Jarres R, von Mackensen S. Health‐related quality of life and health status in persons with haemophilia A with inhibitors: A prospective, multicentre, non‐interventional study (NIS). Haemophilia 2019, 25: 382-391. PMID: 31016855, PMCID: PMC6850115, DOI: 10.1111/hae.13731.
- Aledort L, Carpenter S, Cuker A, Kulkarni R, Recht M, Young G, Leissinger C. Why plasma‐derived factor VIII? Haemophilia 2019, 25: e183-e185. PMID: 30866124, DOI: 10.1111/hae.13705.
- Samuelson Bannow B, Recht M, Négrier C, Hermans C, Berntorp E, Eichler H, Mancuso M, Klamroth R, O'Hara J, Santagostino E, Matsushita T, Kessler C. Factor VIII: Long-established role in haemophilia A and emerging evidence beyond haemostasis. Blood Reviews 2019, 35: 43-50. PMID: 30922616, DOI: 10.1016/j.blre.2019.03.002.
- Winsnes K, Sochacki P, Eriksson C, Shereck E, Recht M, Johnson K, De Mola R, Stork L. Delirium in the pediatric hematology, oncology, and bone marrow transplant population. Pediatric Blood & Cancer 2019, 66: e27640. PMID: 30697919, DOI: 10.1002/pbc.27640.
- Mahlangu J, Oldenburg J, Callaghan M, Shima M, Santagostino E, Moore M, Recht M, Garcia C, Yang R, Lehle M, Macharia H, Asikanius E, Levy G, Kruse‐Jarres R. Bleeding events and safety outcomes in persons with haemophilia A with inhibitors: A prospective, multi‐centre, non‐interventional study. Haemophilia 2018, 24: 921-929. PMID: 30295389, DOI: 10.1111/hae.13612.
- Gruppo R, Malan D, Kapocsi J, Nemes L, Hay C, Boggio L, Chowdary P, Tagariello G, von Drygalski A, Hua F, Scaramozza M, Arkin S, Investigators F, Hermans C, Claes C, Hanes I, Huyghe I, Kantaridis C, da Costa L, Ndongo M, Petit W, Santagostino E, Cannavo A, Fasulo M, Mancuso M, Tosetto A, Castaman G, Candiotto L, Radossi P, Scarpa E, Smith M, Dick A, Robson R, Waaka D, Wynne C, Punt Z, Kavakli K, Balkan C, Duyu M, Goksel S, Karapinar B, Ozyurek A, Saydam G, Karapinar D, Laffan M, Millar C, Suppiah P, Rizleigh C, Chowdary G, Davies J, Fosbury E, Gill S, Pike G, Thachil J, Recht M, Deutsche J, Taylor J, Kalinyak K, Mullins E, Palumbo J, Quinn C, Tarango C, Tarabar S, Chandler P, Deats L, Deshpande S, Epstein N, Hansson A, Pawlak S, Rudin D, Valentino L, Kakodkar N, Simpson M, Fogarty P, Bach T, Chiang E, Adamson J, Glass C, Sidhu N, Tucker‐Greene T. Phase 1, single‐dose escalating study of marzeptacog alfa (activated), a recombinant factor VIIa variant, in patients with severe hemophilia. Journal Of Thrombosis And Haemostasis 2018, 16: 1984-1993. PMID: 30151972, DOI: 10.1111/jth.14247.
- Croteau S, Callaghan M, Davis J, Dunn A, Guerrera M, Khan O, Neufeld E, Raffini L, Recht M, Wang M, Iorio A. Focusing in on use of pharmacokinetic profiles in routine hemophilia care. Research And Practice In Thrombosis And Haemostasis 2018, 2: e12118. PMID: 30046766, PMCID: PMC6046597, DOI: 10.1002/rth2.12118.
- Manco‐Johnson M, Byams V, Recht M, Dudley B, Dupervil B, Aschman D, Oakley M, Kapica S, Voutsis M, Humes S, Kulkarni R, Grant A, Network. O. Community counts: Evolution of a national surveillance system for bleeding disorders. American Journal Of Hematology 2018, 93: e137-e140. PMID: 29473207, PMCID: PMC6145085, DOI: 10.1002/ajh.25076.
- Roberts J, Lattimore S, Recht M, Jackson S, Gue D, Squire S, Robinson K, Price V, Denne M, Richardson S, Rockwood K. Goal Attainment Scaling for haemophilia (GAS‐Hēm): testing the feasibility of a new patient‐centric outcome measure in people with haemophilia. Haemophilia 2018, 24: e199-e206. PMID: 29626387, DOI: 10.1111/hae.13454.
- Buckner T, Batt K, Quon D, Witkop M, Recht M, Kessler C, Baumann K, Hernandez G, Wang M, Cooper D, Kempton C. Assessments of pain, functional impairment, anxiety, and depression in US adults with hemophilia across patient‐reported outcome instruments in the Pain, Functional Impairment, and Quality of Life (P‐FiQ) study. European Journal Of Haematology 2018, 100: 5-13. PMID: 29498784, DOI: 10.1111/ejh.13027.
- Batt K, Boggio L, Neff A, Buckner T, Wang M, Quon D, Witkop M, Recht M, Kessler C, Iyer N, Cooper D. Patient‐reported outcomes and joint status across subgroups of US adults with hemophilia with varying characteristics: Results from the Pain, Functional Impairment, and Quality of Life (P‐FiQ) study. European Journal Of Haematology 2018, 100: 14-24. PMID: 29498783, DOI: 10.1111/ejh.13028.
- Rocheleau A, Khader A, Ngo A, Boehnlein C, McDavitt C, Lattimore S, Recht M, McCarty O, Haley K. Pilot study of novel lab methodology and testing of platelet function in adolescent women with heavy menstrual bleeding. Pediatric Research 2018, 83: 693-701. PMID: 29166373, PMCID: PMC5902421, DOI: 10.1038/pr.2017.298.
- Kempton C, Recht M, Neff A, Wang M, Buckner T, Soni A, Quon D, Witkop M, Boggio L, Gut R, Cooper D. Impact of pain and functional impairment in US adults with haemophilia: Patient‐reported outcomes and musculoskeletal evaluation in the pain, functional impairment and quality of life (P‐FiQ) study. Haemophilia 2017, 24: 261-270. PMID: 29218759, DOI: 10.1111/hae.13377.
- Kempton C, Wang M, Recht M, Neff A, Shapiro A, Soni A, Kulkarni R, Buckner T, Batt K, Iyer N, Cooper D. Reliability of patient-reported outcome instruments in US adults with hemophilia: the Pain, Functional Impairment and Quality of life (P-FiQ) study. Patient Preference And Adherence 2017, 11: 1603-1612. PMID: 29033549, PMCID: PMC5614789, DOI: 10.2147/ppa.s141389.
- Batt K, Recht M, Cooper D, Iyer N, Kempton C. Construct validity of patient-reported outcome instruments in US adults with hemophilia: results from the Pain, Functional Impairment, and Quality of life (P-FiQ) study. Patient Preference And Adherence 2017, 11: 1369-1380. PMID: 28860720, PMCID: PMC5558590, DOI: 10.2147/ppa.s141390.
- Ullman M, Zhang Q, Grosse S, Recht M, Soucie J, Investigators T. Prophylaxis use among males with haemophilia B in the United States. Haemophilia 2017, 23: 910-917. PMID: 28780772, PMCID: PMC5724962, DOI: 10.1111/hae.13317.
- Shatzel J, Azar S, Scherber R, Gay N, Deloughery T, VanSandt A, Kruse‐Jarres R, Recht M, Taylor J. Unexpected pharmacokinetics of recombinant porcine factor VIII in a patient with acquired factor VIII deficiency and spontaneous epidural haematoma. Haemophilia 2017, 23: e453-e456. PMID: 28664642, DOI: 10.1111/hae.13247.
- Kahan S, Cuker A, Kushner R, Maahs J, Recht M, Wadden T, Willis T, Majumdar S, Ungar D, Cooper D. Prevalence and impact of obesity in people with haemophilia: Review of literature and expert discussion around implementing weight management guidelines. Haemophilia 2017, 23: 812-820. PMID: 28636076, DOI: 10.1111/hae.13291.
- Recht M, Rajpurkar M, Chitlur M, d'Oiron R, Zotz R, Di Minno G, Cooper D, Poon M. Independent adjudicator assessments of platelet refractoriness and rFVIIa efficacy in bleeding episodes and surgeries from the multinational Glanzmann's thrombasthenia registry. American Journal Of Hematology 2017, 92: 646-652. PMID: 28370369, DOI: 10.1002/ajh.24741.
- Witkop M, Neff A, Buckner T, Wang M, Batt K, Kessler C, Quon D, Boggio L, Recht M, Baumann K, Gut R, Cooper D, Kempton C. Self‐reported prevalence, description and management of pain in adults with haemophilia: methods, demographics and results from the Pain, Functional Impairment, and Quality of life (P‐FiQ) study. Haemophilia 2017, 23: 556-565. PMID: 28419637, DOI: 10.1111/hae.13214.
- Chitlur M, Rajpurkar M, Recht M, Tarantino M, Yee D, Cooper D, Gunawardena S. Recognition and management of platelet-refractory bleeding in patients with Glanzmann’s thrombasthenia and other severe platelet function disorders. International Journal Of General Medicine 2017, 10: 95-99. PMID: 28435309, PMCID: PMC5388206, DOI: 10.2147/ijgm.s128953.
- Buckner T, Witkop M, Guelcher C, Frey M, Hunter S, Peltier S, Recht M, Walsh C, Kessler C, Owens W, Clark D, Frick N, Rice M, Iyer N, Holot N, Cooper D, Sidonio R. Management of US men, women, and children with hemophilia and methods and demographics of the Bridging Hemophilia B Experiences, Results and Opportunities into Solutions (B‐HERO‐S) study. European Journal Of Haematology 2017, 98: 5-17. PMID: 28319338, DOI: 10.1111/ejh.12854.
- Oleson D, Fox L, Nguyen T, Sochacki P, McCarthy M, Adams E, Recht M. A comparison of two types of ankle supports in men with haemophilia and unilateral ankle pain from arthropathy. Haemophilia 2017, 23: 444-448. PMID: 28220573, DOI: 10.1111/hae.13184.
- Recht M, Chitlur M, Lam D, Sarnaik S, Rajpurkar M, Cooper D, Gunawardena S. Epistaxis as a Common Presenting Symptom of Glanzmann’s Thrombasthenia, a Rare Qualitative Platelet Disorder: Illustrative Case Examples. Case Reports In Emergency Medicine 2017, 2017: 8796425. PMID: 28299211, PMCID: PMC5337314, DOI: 10.1155/2017/8796425.
- Aledort L, Recht M, Kulkarni R, Kobrinsky N. Adult, previously untreated patients remain a significant therapeutic challenge. Journal Of Thrombosis And Haemostasis 2016, 14: 2075-2076. PMID: 27496600, DOI: 10.1111/jth.13434.
- Recht M, Konkle B, Jackson S, Neufeld E, Rockwood K, Pipe S. Recognizing the need for personalization of haemophilia patient‐reported outcomes in the prophylaxis era. Haemophilia 2016, 22: 825-832. PMID: 27581872, DOI: 10.1111/hae.13066.
- Lentz S, Cerqueira M, Janic D, Kempton C, Matytsina I, Misgav M, Oldenburg J, Ozelo M, Recht M, Rosholm A, Savic A, Suzuki T, Tiede A, Santagostino E. Interim results from a large multinational extension trial (guardian™2) using turoctocog alfa for prophylaxis and treatment of bleeding in patients with severe haemophilia A. Haemophilia 2016, 22: e445-e449. PMID: 27291066, DOI: 10.1111/hae.12990.
- Baker‐Groberg S, Lattimore S, Recht M, McCarty O, Haley K. Assessment of neonatal platelet adhesion, activation, and aggregation. Journal Of Thrombosis And Haemostasis 2016, 14: 815-827. PMID: 26806373, PMCID: PMC4828266, DOI: 10.1111/jth.13270.
- Mahlangu J, Weldingh K, Lentz S, Kaicker S, Karim F, Matsushita T, Recht M, Tomczak W, Windyga J, Ehrenforth S, Knobe K, Investigators F, Weltermann A, de Paula E, Cerqueira M, Zupancic‐Salek S, Katsarou O, Economou M, Nemes L, Boda Z, Santagostino E, Tagariello G, Hanabusa H, Fukutake K, Shima M, Serban M, Elezovic I, Savic A, Shen M, Chuansumrit A, Angchaisuksiri P, Kavakli K, Sasmaz I, Madan B, Giangrande P, Kempton C, Young G, Quon D, Ameri A, Kuriakose P, Obzut D, Wang M, Ortiz I. Changes in the amino acid sequence of the recombinant human factor VIIa analog, vatreptacog alfa, are associated with clinical immunogenicity. Journal Of Thrombosis And Haemostasis 2015, 13: 1989-1998. PMID: 26362483, DOI: 10.1111/jth.13141.
- Goldenberg N, Abshire T, Blatchford P, Fenton L, Halperin J, Hiatt W, Kessler C, Kittelson J, Manco‐Johnson M, Spyropoulos A, Steg P, Stence N, Turpie A, Schulman S, Punzalan R, Wang M, Jaffray J, Young G, Rajpurkar M, Carpenter S, Diab Y, Verdun N, Tarango C, Acharya S, Torres M, Kucine N, Mitchell B, Shah N, Thornburg C, Takemoto C, Kulkarni R, O'Brien S, Haley K, Recht M, Knoll C, Thornburg C, Geddis A, Ahuja S, Simpson M, Srivaths L, Journeycake J, Zia A. Multicenter randomized controlled trial on Duration of Therapy for Thrombosis in Children and Young Adults (the Kids‐DOTT trial): pilot/feasibility phase findings. Journal Of Thrombosis And Haemostasis 2015, 13: 1597-1605. PMID: 26118944, PMCID: PMC4561031, DOI: 10.1111/jth.13038.
- Gay N, Lee S, Liel M, Sochacki P, Recht M, Taylor J. Increased fracture rates in people with haemophilia: a 10‐year single institution retrospective analysis. British Journal Of Haematology 2015, 170: 584-586. PMID: 25659575, DOI: 10.1111/bjh.13312.
- Nathwani A, Reiss U, Tuddenham E, Rosales C, Chowdary P, McIntosh J, Della Peruta M, Lheriteau E, Patel N, Raj D, Riddell A, Pie J, Rangarajan S, Bevan D, Recht M, Shen Y, Halka K, Basner-Tschakarjan E, Mingozzi F, High K, Allay J, Kay M, Ng C, Zhou J, Cancio M, Morton C, Gray J, Srivastava D, Nienhuis A, Davidoff A. Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B. The New England Journal Of Medicine 2014, 371: 1994-2004. PMID: 25409372, PMCID: PMC4278802, DOI: 10.1056/nejmoa1407309.
- Maahs J, Donkin J, Recht M, Cooper D. Mixing and administration times of bypassing agents: observations from the Dosing Observational Study in Hemophilia (DOSE). Journal Of Blood Medicine 2014, 5: 153-156. PMID: 25187744, PMCID: PMC4149444, DOI: 10.2147/jbm.s61859.
- Recht M, Neufeld E, Sharma V, Solem C, Pickard A, Gut R, Cooper D. Impact of Acute Bleeding on Daily Activities of Patients with Congenital Hemophilia with Inhibitors and Their Caregivers and Families: Observations from the Dosing Observational Study in Hemophilia (DOSE). Value In Health 2014, 17: 744-748. PMID: 25236999, DOI: 10.1016/j.jval.2014.07.003.
- Rajpurkar M, Chitlur M, Recht M, Cooper D. Use of recombinant activated factor VII in patients with Glanzmann's thrombasthenia: a review of the literature. Haemophilia 2014, 20: 464-471. PMID: 24948404, DOI: 10.1111/hae.12473.
- Haley K, Recht M, McCarty O. Neonatal platelets: mediators of primary hemostasis in the developing hemostatic system. Pediatric Research 2014, 76: 230-237. PMID: 24941213, PMCID: PMC4348010, DOI: 10.1038/pr.2014.87.
- Haley K, Russell T, Boshkov L, Leger R, Garratty G, Recht M, Nazemi K. Fatal carboplatin-induced immune hemolytic anemia in a child with a brain tumor. Journal Of Blood Medicine 2014, 5: 55-58. PMID: 24868179, PMCID: PMC4031206, DOI: 10.2147/jbm.s59192.
- Adams E, Deutsche J, Okoroh E, Owens‐McAlister S, Majumdar S, Ullman M, Damiano M, Recht M, Group T. An inventory of healthy weight practices in federally funded haemophilia treatment centres in the United States. Haemophilia 2014, 20: 639-643. PMID: 24629074, PMCID: PMC4484574, DOI: 10.1111/hae.12385.
- Recht M, Liel M, Turner R, Klein R, Taylor J. The bone disease associated with factor VIII deficiency in mice is secondary to increased bone resorption. Haemophilia 2013, 19: 908-912. PMID: 23731369, DOI: 10.1111/hae.12195.
- Soucie J, Monahan P, Kulkarni R, De Staercke C, Recht M, Chitlur M, Gruppo R, Hooper W, Kessler C, Manco‐Johnson M, Powell J, Pyle M, Riske B, Sabio H, Trimble S. Evidence for the continued transmission of parvovirus B19 in patients with bleeding disorders treated with plasma‐derived factor concentrates. Transfusion 2013, 53: 1143-1144. PMID: 23659532, DOI: 10.1111/trf.12153.
- Lentz S, Misgav M, Ozelo M, Šalek S, Veljkovic D, Recht M, Cerqueira M, Tiede A, Brand B, Mancuso M, Seremetis S, Lindblom A, Martinowitz U. Results from a large multinational clinical trial (guardian™1) using prophylactic treatment with turoctocog alfa in adolescent and adult patients with severe haemophilia A: safety and efficacy. Haemophilia 2013, 19: 691-697. PMID: 23647704, DOI: 10.1111/hae.12159.
- Lane J, McLaren P, Dorrell L, Shianna K, Stemke A, Pelak K, Moore S, Oldenburg J, Alvarez-Roman M, Angelillo-Scherrer A, Boehlen F, Bolton-Maggs P, Brand B, Brown D, Chiang E, Cid-Haro A, Clotet B, Collins P, Colombo S, Dalmau J, Fogarty P, Giangrande P, Gringeri A, Iyer R, Katsarou O, Kempton C, Kuriakose P, Lin J, Makris M, Manco-Johnson M, Tsakiris D, Martinez-Picado J, Mauser-Bunschoten E, Neff A, Oka S, Oyesiku L, Parra R, Peter-Salonen K, Powell J, Recht M, Shapiro A, Stine K, Talks K, Telenti A, Wilde J, Yee T, Wolinsky S, Martinson J, Hussain S, Bream J, Jacobson L, Carrington M, Goedert J, Haynes B, McMichael A, Goldstein D, Fellay J, Immunology F. A genome-wide association study of resistance to HIV infection in highly exposed uninfected individuals with hemophilia A. Human Molecular Genetics 2013, 22: 1903-1910. PMID: 23372042, PMCID: PMC3613165, DOI: 10.1093/hmg/ddt033.
- Soucie J, De Staercke C, Monahan P, Recht M, Chitlur M, Gruppo R, Hooper W, Kessler C, Kulkarni R, Manco‐Johnson M, Powell J, Pyle M, Riske B, Sabio H, Trimble S, Network H. Evidence for the transmission of parvovirus B19 in patients with bleeding disorders treated with plasma‐derived factor concentrates in the era of nucleic acid test screening. Transfusion 2012, 53: 1217-1225. PMID: 22998193, PMCID: PMC4519820, DOI: 10.1111/j.1537-2995.2012.03907.x.
- Neufeld E, Recht M, Sabio H, Saxena K, Solem C, Pickard A, Gut R, Cooper D. Effect of Acute Bleeding on Daily Quality of Life Assessments in Patients with Congenital Hemophilia with Inhibitors and Their Families: Observations from the Dosing Observational Study in Hemophilia. Value In Health 2012, 15: 916-925. PMID: 22999142, DOI: 10.1016/j.jval.2012.05.005.
- Auerswald G, Thompson A, Recht M, Brown D, Liesner R, Guzmán-Becerra N, Dyck-Jones J, Ewenstein B, Abbuehl B. Experience of Advate rAHF-PFM in previously untreated patients and minimally treated patients with haemophilia A. Thrombosis And Haemostasis 2012, 107: 1072-1082. PMID: 22476554, PMCID: PMC6292131, DOI: 10.1160/th11-09-0642.
- Liel M, Greenberg D, Recht M, Vanek C, Klein R, Taylor J. Decreased bone density and bone strength in a mouse model of severe factor VIII deficiency. British Journal Of Haematology 2012, 158: 140-143. PMID: 22469061, DOI: 10.1111/j.1365-2141.2012.09101.x.
- Chiu Y, Drolet B, Blei F, Carcao M, Fangusaro J, Kelly M, Krol A, Lofgren S, Mancini A, Metry D, Recht M, Silverman R, Tom W, Pope E. Variable response to propranolol treatment of kaposiform hemangioendothelioma, tufted angioma, and Kasabach–Merritt phenomenon. Pediatric Blood & Cancer 2012, 59: 934-938. PMID: 22648868, PMCID: PMC3528889, DOI: 10.1002/pbc.24103.
- Bradeen H, Shehab S, Recht M. Iron Metabolism and Iron Deficiency Anemia. 2012, 2963-2968. DOI: 10.1007/978-3-642-02202-9_318.
- Flood V, Recht M. Autoimmune Hemolytic Anemia. 2012, 2969-2974. DOI: 10.1007/978-3-642-02202-9_319.
- Richard N, Haley K, Recht M. Thalassemia. 2012, 3029-3036. DOI: 10.1007/978-3-642-02202-9_326.
- Wong T, Majumdar S, Adams E, Bergman S, Damiano M, Deutsche J, Recht M, Group H. Overweight and Obesity in Hemophilia A Systematic Review of the Literature. American Journal Of Preventive Medicine 2011, 41: s369-s375. PMID: 22099360, DOI: 10.1016/j.amepre.2011.09.008.
- Grace R, Bennett C, Ritchey A, Jeng M, Thornburg C, Lambert M, Neier M, Recht M, Kumar M, Blanchette V, Klaassen R, Buchanan G, Kurth M, Nugent D, Thompson A, Stine K, Kalish L, Neufeld E. Response to steroids predicts response to rituximab in pediatric chronic immune thrombocytopenia. Pediatric Blood & Cancer 2011, 58: 221-225. PMID: 21674758, PMCID: PMC3863944, DOI: 10.1002/pbc.23130.
- RECHT M, POLLMANN H, TAGLIAFERRI A, MUSSO R, JANCO R, NEUMAN W. A retrospective study to describe the incidence of moderate to severe allergic reactions to factor IX in subjects with haemophilia B. Haemophilia 2011, 17: 494-499. PMID: 21518148, DOI: 10.1111/j.1365-2516.2011.02436.x.
- SOUCIE J, WANG C, SIDDIQI A, KULKARNI R, RECHT M, KONKLE B, NETWORK T. The longitudinal effect of body adiposity on joint mobility in young males with Haemophilia A. Haemophilia 2011, 17: 196-203. PMID: 21332880, DOI: 10.1111/j.1365-2516.2010.02400.x.
- Wong T, Recht M. Current Options and New Developments in the Treatment of Haemophilia. Drugs 2011, 71: 305-320. PMID: 21319868, DOI: 10.2165/11585340-000000000-00000.
- Recht M. Thrombocytopenia and Anemia in Infants and Children. Emergency Medicine Clinics Of North America 2009, 27: 505-523. PMID: 19646651, DOI: 10.1016/j.emc.2009.04.009.
- RECHT M, NEMES L, MATYSIAK M, MANCO‐JOHNSON M, LUSHER J, SMITH M, MANNUCCI P, HAY C, ABSHIRE T, O’BRIEN A, HAYWARD B, UDATA C, ROTH D, ARKIN S. Clinical evaluation of moroctocog alfa (AF‐CC), a new generation of B‐domain deleted recombinant factor VIII (BDDrFVIII) for treatment of haemophilia A: demonstration of safety, efficacy, and pharmacokinetic equivalence to full‐length recombinant factor VIII. Haemophilia 2009, 15: 869-880. PMID: 19473411, DOI: 10.1111/j.1365-2516.2009.02027.x.
- SPENCER M, WODRICH D, SCHULTZ W, WAGNER L, RECHT M. Inattention, hyperactivity‐impulsivity, academic skills and psychopathology in boys with and without haemophilia. Haemophilia 2009, 15: 701-706. PMID: 19298375, DOI: 10.1111/j.1365-2516.2009.01993.x.
- VALENTINO L, RECHT M, DIPAOLA J, SHAPIRO A, PIPE S, EWING N, URGO J, BULLOCK T, SIMMONS M, DEGUZMAN C. Experience with a third generation recombinant factor VIII concentrate (Advate®) for immune tolerance induction in patients with haemophilia A. Haemophilia 2009, 15: 718-726. PMID: 19298383, DOI: 10.1111/j.1365-2516.2008.01960.x.
- GERSTNER G, DAMIANO M, TOM A, WORMAN C, SCHULTZ W, RECHT M, STOPECK A. Prevalence and risk factors associated with decreased bone mineral density in patients with haemophilia. Haemophilia 2009, 15: 559-565. PMID: 19187193, DOI: 10.1111/j.1365-2516.2008.01963.x.
- Manco-Johnson M, Abshire T, Shapiro A, Riske B, Hacker M, Kilcoyne R, Ingram J, Manco-Johnson M, Funk S, Jacobson L, Valentino L, Hoots W, Buchanan G, DiMichele D, Recht M, Brown D, Leissinger C, Bleak S, Cohen A, Mathew P, Matsunaga A, Medeiros D, Nugent D, Thomas G, Thompson A, McRedmond K, Soucie J, Austin H, Evatt B. Prophylaxis versus Episodic Treatment to Prevent Joint Disease in Boys with Severe Hemophilia. The New England Journal Of Medicine 2007, 357: 535-544. PMID: 17687129, DOI: 10.1056/nejmoa067659.
- LAMBERT T, RECHT M, VALENTINO L, POWELL J, UDATA C, SULLIVAN S, ROTH D. Reformulated BeneFix®: efficacy and safety in previously treated patients with moderately severe to severe haemophilia B. Haemophilia 2007, 13: 233-243. PMID: 17498071, DOI: 10.1111/j.1365-2516.2007.01458.x.
- Hay C, Recht M, Carcao M, Reipert B. Current and Future Approaches to Inhibitor Management and Aversion. Seminars In Thrombosis And Hemostasis 2006, 32: 015-021. PMID: 16804831, DOI: 10.1055/s-2006-946910.
- Wodrich D, Recht M, Gradowski M, Wagner L. Is attention deficit hyperactivity disorder over‐represented among HIV‐seronegative boys with haemophilia? Preliminary results from our centre. Haemophilia 2003, 9: 593-597. PMID: 14511300, DOI: 10.1046/j.1365-2516.2003.00790.x.
- Rincón M, Enslen H, Raingeaud J, Recht M, Zapton T, Su M, Penix L, Davis R, Flavell R. Interferon‐γ expression by Th1 effector T cells mediated by the p38 MAP kinase signaling pathway. The EMBO Journal 1998, 17: 2817-2829. PMID: 9582275, PMCID: PMC1170622, DOI: 10.1093/emboj/17.10.2817.
- Rinder HM, Tracey JB, Recht M, DeCastro L, Rinder CS, McHugh C, Smith BR. Differences in Platelet α-granule Release between Normals and Immune Thrombocytopenic Patients and between Young and Old Platelets. Thrombosis And Haemostasis 1998, 80: 457-462. PMID: 9759627, DOI: 10.1055/s-0037-1615229.
- Pediatric Specialty CenterTrumbull Pediatric Specialty Center5520 Park Avenue, Ste 600Trumbull, CT 06611
- Smilow Cancer HospitalSmilow Cancer Hospital at Yale New Haven35 Park StreetNew Haven, CT 06511
- Pediatric Specialty CenterOld Saybrook Medical Center633 Middlesex Turnpike, Ste 110Old Saybrook, CT 06475
Biography
Michael Recht, MD, PhD, is a pediatric hematologist who focuses on treating children, adolescents, and young adults with bleeding and clotting disorders.
Dr. Recht is a professor of clinical pediatrics at Yale School of Medicine. He has been actively involved in more than 110 clinical trials, including research on gene therapy for hemophilia. Dr. Recht also serves as the chief medical and scientific officer for the National Bleeding Disorders Foundation. In this role, he helps shape the scientific direction and research strategy of the organization, working to advance the understanding and treatment of bleeding disorders. Dr. Recht received his medical and doctoral degrees from the University of Wisconsin-Madison. He completed his residency in pediatrics and fellowship in pediatric hematology-oncology at Yale New Haven Hospital.
Titles
- Professor of Clinical Pediatrics (Hematology/Oncology)
- Chief Medical and Scientific Officer, National Hemophilia Foundation, National Hemophilia Foundation
Education & Training
- MBAOregon Health & Science University/Portland State University (2016)
- FellowYale University School of Medicine (1998)
- ResidentYale New Haven Hospital (1995)
- MDUniversity of Wisconsin-Madison (1992)
- PhDUniversity of Wisconsin-Madison (1990)
Additional Information
- Chrisentery-Singleton T, Acharya S, Ahuja S, Amos L, Chitlur M, Daoud N, Eason A, Escobar M, Fedor C, Gupta S, Kuriakose P, Nasr S, Pennington S, Pruthi R, Recht M, Robertson A, Quon D, Wheeler A, Reding M. Safety and real-world effectiveness of eptacog beta with emicizumab prophylaxis: an interim analysis of the ATHN 16 study. Blood Vessels Thrombosis & Hemostasis 2026, 3: 100169. DOI: 10.1016/j.bvth.2026.100169.
- Czura C, Weyand A, Baldwin M, Recht M, Benner C, Harada K, Wade B, Luellen M, Darrow M, McWade M, Covalin A, Khodaparast N. A novel transcutaneous auricular neurostimulation electrode configuration for treatment of heavy menstrual bleeding: an open-label trial. Bioelectronic Medicine 2026, 12: 10. PMID: 41933398, PMCID: PMC13049727, DOI: 10.1186/s42234-026-00203-1.
- Pipe S, Miesbach W, Recht M, Leebeek F, Key N, Castaman G, Lattimore S, Coppens M, Le Quellec S, Mahajan V, Gill S, Drelich D, Monahan P. Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia B. The New England Journal Of Medicine 2025, 394: 463-474. PMID: 41358585, DOI: 10.1056/nejmoa2514332.
- Buckner T, Carpenter S, Daoud N, Kempton C, Lee L, Malec L, McLean T, Morton P, O'Neill C, Staber J, Wang M, Croteau S, Recht M. Safety and Effectiveness of Emicizumab in People With Haemophilia A Enrolled in the ATHN 7 Haemophilia Natural History Study. Haemophilia 2025, 32: 63-70. PMID: 41220279, PMCID: PMC12904170, DOI: 10.1111/hae.70151.
- Czura C, Weyand A, Baldwin M, Recht M, McWade M, Covalin A, Khodaparast N. Transcutaneous auricular neurostimulation to reduce heavy menstrual bleeding in women with and without von Willebrand disease. Frontiers In Medicine 2025, 12: 1664433. PMID: 41133152, PMCID: PMC12540315, DOI: 10.3389/fmed.2025.1664433.
- Klamroth R, Recht M, Key N, Miesbach W, Pipe S, Kaczmarek R, Drelich D, Salazar B, Le Quellec S, Monahan P, Galante N, van der Valk P, Tarrant J. Natural history of preexisting AAV5 antibodies in adults with hemophilia B during the lead-in of the etranacogene dezaparvovec phase 3 study. Molecular Therapy Advances 2025, 33: 101568. PMID: 40969675, PMCID: PMC12441693, DOI: 10.1016/j.omtm.2025.101568.
- Chandler M, Moulton T, Charafi L, Charlet J, Recht M. Effectiveness of Octocog Alfa (BAY 81‐8973) to Treat People With Haemophilia A Enrolled in the ATHNdataset, Including Under‐Represented Subgroups. European Journal Of Haematology 2025, 115: 484-492. PMID: 40770897, PMCID: PMC12505839, DOI: 10.1111/ejh.70016.
- Valentino L, Santaella M, Witkop M, Stanhope R, Valadez S, Carlson S, Benasutti H, DiMichele D, Recht M. The Bleeding Disorders Research Collaborative. Blood Vessels Thrombosis & Hemostasis 2025, 2: 100099. PMID: 41070002, PMCID: PMC12506547, DOI: 10.1016/j.bvth.2025.100099.
- von Drygalski A, Gomez E, Giermasz A, Castaman G, Key N, Lattimore S, Leebeek F, Miesbach W, Recht M, Monahan P, Le Quellec S, Pipe S. Completion of phase 2b trial of etranacogene dezaparvovec gene therapy in patients with hemophilia B over 5 years. Blood Advances 2025, 9: 3543-3552. PMID: 40188458, PMCID: PMC12275190, DOI: 10.1182/bloodadvances.2024015291.
- Madan B, Ozelo M, Kenet G, Chou S, Dashiell-Aje E, Robinson T, Mahlangu J, Recht M, Careta F, Ruiz A, Fletcher S, Goshen D. Plain language summary of 4-year results of the GENEr8-1 clinical trial of valoctocogene roxaparvovec gene therapy for hemophilia A. Future Rare Diseases 2025, 5: 2522071. DOI: 10.1080/23995270.2025.2522071.
- Buckner T, Kessler C, Castaman G, Hermans C, Jiménez‐Yuste V, Mahlangu J, Miesbach W, Oldenburg J, Recht M, Valentino L, Wheeler A, Pipe S. Pain Reduction Following Eptacog Beta Treatment of Bleeding Episodes in Adolescents and Adults With Haemophilia A or B Complicated by Inhibitors. Haemophilia 2025, 31: 713-721. PMID: 40534395, DOI: 10.1111/hae.70077.
- Thornburg C, van den Berg H, Chandler M, Malec L, Manuel M, O’Neill C, Recht M, Taggart E, Carpenter S, group A, Knoll C, Malec L, Wang M, Guerrera M, Tarango C, Sidonio R, Rodriguez N, Friedman K, Shapiro A, Yaish H, Carpenter S, Janbain M, Grabowski E, Pruthi R, Haley K, Thornburg C, Ahuja S, Simpson M, Reiss U, Lucas T, Balasa V, Wheeler A. Inhibitor development and clinical characteristics in children with severe hemophilia A in the ATHN 8 US cohort study. Blood Vessels Thrombosis & Hemostasis 2025, 2: 100082. PMID: 40918739, PMCID: PMC12412393, DOI: 10.1016/j.bvth.2025.100082.
- Konkle B, Peyvandi F, Foster G, Hermans C, La Mura V, Leavitt A, Lillicrap D, Mahlangu J, Ozelo M, Pipe S, Recht M, Srivastava A, Young G, Miesbach W. Corticosteroid use to mitigate transaminitis-associated decline in FVIII levels following valoctocogene roxaparvovec gene therapy: clinical practice guidance. Journal Of Thrombosis And Haemostasis 2025, 23: 2086-2094. PMID: 40090623, DOI: 10.1016/j.jtha.2025.02.042.
- Chrisentery‐Singleton T, Gattone P, Gerber C, Mills K, Miles M, Rotellini D, Santaella M, Valentino L, Watson C, Recht M. American Thrombosis and Hemostasis Network: National Bleeding Disorders Foundation Data Commons: Better Together. Haemophilia 2025, 31: 589-593. PMID: 39982786, DOI: 10.1111/hae.70011.
- Valentino L, Santaella M, Carlson S, Recht M. Contemporary approaches to treat people with hemophilia: what’s new and what’s not? Research And Practice In Thrombosis And Haemostasis 2025, 9: 102696. PMID: 40084158, PMCID: PMC11905833, DOI: 10.1016/j.rpth.2025.102696.
- Dunn A, Dargaud Y, Abajas Y, Carcao M, Castaman G, Giermasz A, Hermans C, Jiménez‐Yuste V, Lewandowska M, Mahlangu J, Meeks S, Miesbach W, Recht M, Salinas V, Chrisentery‐Singleton T, Bonzo D, Mitchell I, Wilkinson T, Young G. Bleed treatment with eptacog beta (rFVIIa) results in a low incidence of rebleeding in adult and adolescent patients with haemophilia A or B with inhibitors. Haemophilia 2024, 31: 78-86. PMID: 39676340, PMCID: PMC11780187, DOI: 10.1111/hae.15109.
- Skinner M, Albisetti M, Ardila J, Astermark J, Blatny J, Carcao M, Chowdary P, Connell N, Crato M, Dargaud Y, d'Oiron R, Dunn A, Escobar M, Escuriola‐Ettingshausen C, Gouider E, Harroche A, Hermans C, Jimenez‐Yuste V, Kaczmarek R, Kenet G, Khoo L, Klamroth R, Langer F, Lillicrap D, Mahlangu J, Male C, Matsushita T, Meunier S, Miesbach W, Nolan B, Oldenburg J, O'Mahony B, Ozelo M, Pierce G, Ramos G, Recht M, Romero‐Lux O, Rotellini D, Santoro R, Singleton T, Srivastava A, Susen S, Talks K, Tran H, Valentino L, Windyga J, Yang R, Mancuso M, also on behalf of AICE A. Contrasting Approaches in the Implementation of GRADE Methodology in Guidelines for Haemophilia and Von Willebrand Disease. Haemophilia 2024 PMID: 39648854, DOI: 10.1111/hae.15136.
- Albisetti M, Ardila J, Astermark J, Blatny J, Carcao M, Chowdary P, Connell N, Crato M, Dargaud Y, d'Oiron R, Dunn A, Escobar M, Ettingshausen C, Fischer K, Gouider E, Harroche A, Hermans C, Jimenez‐Yuste V, Kaczmarek R, Kenet G, Khoo L, Klamroth R, Langer F, Lillicrap D, Mahlangu J, Male C, Mancuso M, Matsushita T, Meunier S, Miesbach W, Nolan B, Oldenburg J, O'Mahony B, Ozelo M, Pierce G, Ramos G, Recht M, Romero‐Lux O, Rotellini D, Santoro R, Singleton T, Skinner M, Srivastava A, Susen S, Talks K, Tran H, Valentino L, Windyga J, Yang R, also on behalf of AICE A. International Society on Thrombosis and Haemostasis Clinical Practice Guideline for Treatment of Congenital Haemophilia—A Critical Appraisal. Haemophilia 2024 PMID: 39642092, DOI: 10.1111/hae.15135.
- Chandler M, Moulton T, Charafi L, Charlet J, Recht M. Effectiveness of Damoctocog Alfa Pegol to Treat Patients With Hemophilia A Enrolled in the ATHNdataset. European Journal Of Haematology 2024, 114: 448-457. PMID: 39558414, PMCID: PMC11798759, DOI: 10.1111/ejh.14337.
- Youkhana K, Batsuli G, Acharya S, Khan O, Tran D, Dvorak A, Recht M, Young G, Sidonio R, Abajas Y. Real‐world effectiveness of eptacog beta in patients with haemophilia and inhibitors: A multi‐institutional case series. Haemophilia 2024, 30: 1321-1331. PMID: 39297369, PMCID: PMC11659498, DOI: 10.1111/hae.15094.
- DeSancho M, Suvar E, Roberts J, Tarantino M, Schwartz J, Callis J, Recht M. Hereditary antithrombin deficiency pilot project registry from the American Thrombosis and Hemostasis Network. Journal Of Thrombosis And Haemostasis 2024, 22: 3183-3190. PMID: 39151704, DOI: 10.1016/j.jtha.2024.07.026.
- Pierce G, O'Mahony B, Kaczmarek R, Skinner M, Makris M, Peyvandi F, Srivastava A, Hermans C, World Federation of Hemophilia Coagulation Products Supply S, Crato M, Dunn A, Gouider E, Mahlangu J, Page D, Pipe S, Recht M, Sannie T, Schaefer N, Schlenkrich U, Garrido C. Risk of harm to people with haemophilia from the 2023 WHO Essential Medicines List. The Lancet Haematology 2024, 11: e638-e640. PMID: 39116903, DOI: 10.1016/s2352-3026(24)00223-0.
- Nolan B, Recht M, Rendo P, Falk A, Foster M, Casiano S, Rauch A, Shapiro A. Prophylaxis with recombinant factor IX Fc fusion protein reduces the risk of bleeding and delays time to first spontaneous bleed event in previously untreated patients with haemophilia B: A post hoc analysis of the PUPs B‐LONG study. European Journal Of Haematology 2024, 113: 485-492. PMID: 38922990, DOI: 10.1111/ejh.14252.
- Hu J, Chandler M, Manuel C, Caicedo J, Denne M, Ewenstein B, Mokdad A, Xing S, Recht M. Risk of Intracranial Hemorrhage in Persons with Hemophilia A in the United States: Real-World Retrospective Cohort Study Using the ATHNdataset. Journal Of Blood Medicine 2024, 15: 191-205. PMID: 38699197, PMCID: PMC11063465, DOI: 10.2147/jbm.s443380.
- Itzler R, Buckner T, Leebeek F, Miller J, Recht M, Drelich D, Monahan P, Pipe S. Effect of etranacogene dezaparvovec on quality of life for severe and moderately severe haemophilia B participants: Results from the phase III HOPE‐B trial 2 years after gene therapy. Haemophilia 2024, 30: 709-719. PMID: 38462823, DOI: 10.1111/hae.14977.
- Coppens M, Pipe S, Miesbach W, Astermark J, Recht M, van der Valk P, Ewenstein B, Pinachyan K, Galante N, Le Quellec S, Monahan P, Leebeek F, Investigators H, Castaman G, Crary S, Escobar M, Gomez E, Haley K, Hermans C, Kampmann P, Kazmi R, Key N, Klamroth R, Konkle B, Kruse-Jarres R, Lattimore S, Lemons R, Meijer K, O'Connell N, Quon D, Raheja P, Symington E, Verhamme P, Visweshwar N, von Drygalski A, Wang M, Wheeler A, White S, Young G. Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial. The Lancet Haematology 2024, 11: e265-e275. PMID: 38437857, DOI: 10.1016/s2352-3026(24)00006-1.
- Ragni M, Callis J, Daoud N, Hu B, Manuel M, Santos J, Schwartz J, Friedman K, Kouides P, Kuriakose P, Leavitt A, Lim M, Machin N, Recht M, Chrisentery‐Singleton T. Observational cohort study of long‐term outcomes of liver transplantation in haemophilia. Haemophilia 2023, 30: 87-97. PMID: 38111071, DOI: 10.1111/hae.14910.
- von Drygalski A, Gomez E, Giermasz A, Castaman G, Key N, Lattimore S, Leebeek F, Miesbach W, Recht M, Gut R, Dolmetsch R, Monahan P, Le Quellec S, Pipe S. Stable and durable factor IX levels in hemophilia B patients over 3 years post etranacogene dezaparvovec gene therapy. Blood Advances 2023, 7: 5671-5679. PMID: 36490302, PMCID: PMC10539871, DOI: 10.1182/bloodadvances.2022008886.
- Valentino L, Witkop M, Santaella M, DiMichele D, Recht M. The National Hemophilia Foundation State of the Science Research Summit initiative: executive summary. Expert Review Of Hematology 2023, 16: 129-134. PMID: 36920857, DOI: 10.1080/17474086.2023.2181782.
- Valentino L, Witkop M, Santaella M, DiMichele D, Recht M. The National Hemophilia Foundation’s State of the Science Research Summit: the foundation of a national research blueprint for inherited bleeding disorders. Expert Review Of Hematology 2023, 16: 1-5. PMID: 36920858, DOI: 10.1080/17474086.2023.2178412.
- Nugent D, Acharya S, Baumann K, Bedrosian C, Bialas R, Brown K, Corzo D, Haidar A, Hayward C, Marks P, Menegatti M, Miller M, Nammacher K, Palla R, Peltier S, Pruthi R, Recht M, Sørensen B, Tarantino M, Wolberg A, Shapiro A. Building the foundation for a community-generated national research blueprint for inherited bleeding disorders: research priorities for ultra-rare inherited bleeding disorders. Expert Review Of Hematology 2023, 16: 55-70. PMID: 36920862, PMCID: PMC10020868, DOI: 10.1080/17474086.2023.2175661.
- Messenger H, Kulkarni R, Recht M, He C. A Retrospective Analysis of the American Thrombosis and Hemostasis Network Dataset Describing Outcomes of Dental Extractions in Persons with Hemophilia. Journal Of Clinical Medicine 2023, 12: 1839. PMID: 36902626, PMCID: PMC10002874, DOI: 10.3390/jcm12051839.
- Van der Valk P, Pipe S, Key N, Castaman G, Kampmann P, O’Connell N, Hart D, Kazmi R, Astermark J, Klamroth R, Lemons R, Visweshwar N, von Drygalski A, Young G, Escobar M, Gomez E, Symington E, Wang M, Wheeler A, Gut R, Cooper D, Li Y, Goldstein B, Monahan P, Leebeek F, Hermans C, Dolmetsch R, Lattimore S, Peerlinck K, Meijer K, Crary S, Kruse-Jarres R, Quon D, Liu Y, Recht M, Miesbach W, Coppens M, Pasi K. Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B. The New England Journal Of Medicine 2023, 388: 706-718. PMID: 36812434, DOI: 10.1056/nejmoa2211644.
- Parker K, Durben N, Oleson D, Yu Y, Lim J, Recht M, Lindemulder S. Hopping as an Indicator of Chemotoxicity: Gait Analysis in Patients With Leukemia and Lymphoma. Journal Of Pediatric Hematology/Oncology 2023, 45: e582-e589. PMID: 36898017, DOI: 10.1097/mph.0000000000002645.
- Corrales-Medina F, Raffini L, Recht M, Santos J, Thornburg C, Davila J, Investigators A. Direct oral anticoagulants in pediatric venous thromboembolism: Experience in specialized pediatric hemostasis centers in the United States. Research And Practice In Thrombosis And Haemostasis 2022, 7: 100001. PMID: 36970740, PMCID: PMC10031368, DOI: 10.1016/j.rpth.2022.100001.
- Johnsen J, Fletcher S, Dove A, McCracken H, Martin B, Kircher M, Josephson N, Shendure J, Ruuska S, Valentino L, Pierce G, Watson C, Cheng D, Recht M, Konkle B. Results of genetic analysis of 11 341 participants enrolled in the My Life, Our Future hemophilia genotyping initiative in the United States. Journal Of Thrombosis And Haemostasis 2022, 20: 2022-2034. PMID: 35770352, DOI: 10.1111/jth.15805.
- Roberts J, Richardson S, Miles M, Stanley J, Chapman C, Denne M, Caicedo J, Rockwood K, Recht M. The GOAL‐Hēm journey: Shared decision making and patient‐centred outcomes. Haemophilia 2022, 28: 784-795. PMID: 35728103, PMCID: PMC9546188, DOI: 10.1111/hae.14608.
- Valentino L, Witkop M, Santaella M, DiMichele D, Recht M. Building the blueprint: Formulating a community‐generated national plan for future research in inherited bleeding disorders. Haemophilia 2022, 28: 760-768. PMID: 35700441, PMCID: PMC9546016, DOI: 10.1111/hae.14588.
- Rauch A, Valentino L, Mills K, Witkop M, Santaella M, DiMichele D, Recht M, Susen S. Big picture initiatives in bleeding disorders. Haemophilia 2022, 28: 53-60. PMID: 35521733, DOI: 10.1111/hae.14532.
- Pipe S, Hermans C, Chitlur M, Carcao M, Castaman G, Davis J, Ducore J, Dunn A, Escobar M, Journeycake J, Khan O, Mahlangu J, Meeks S, Mitha I, Négrier C, Nowak‐Göttl U, Recht M, Chrisentery‐Singleton T, Stasyshyn O, Vilchevska K, Martinez L, Wang M, Windyga J, Young G, Alexander W, Bonzo D, Macie C, Mitchell I, Sauty E, Wilkinson T, Shapiro A. Eptacog beta efficacy and safety in the treatment and control of bleeding in paediatric subjects (<12 years) with haemophilia A or B with inhibitors. Haemophilia 2022, 28: 548-556. PMID: 35475308, PMCID: PMC9542908, DOI: 10.1111/hae.14563.
- Recht M, He C, Chen E, Cheng D, Solari P, Hinds D. Resource utilization and treatment costs of patients with severe hemophilia A: Real‐world data from the ATHNdataset. EJHaem 2022, 3: 341-352. PMID: 35846041, PMCID: PMC9176109, DOI: 10.1002/jha2.412.
- Burke T, Shaikh A, Ali T, Li N, Curtis R, Diego D, Recht M, Sannie T, Skinner M, O’Hara J. Association of factor expression levels with health-related quality of life and direct medical costs for people with haemophilia B. Journal Of Medical Economics 2022, 25: 386-392. PMID: 35253589, DOI: 10.1080/13696998.2022.2049552.
- Goldenberg N, Kittelson J, Abshire T, Bonaca M, Casella J, Dale R, Halperin J, Hamblin F, Kessler C, Manco-Johnson M, Sidonio R, Spyropoulos A, Steg P, Turpie A, Schulman S, French J, Fargo J, Crary S, Kumar R, Grace R, Trenor C, Wilson H, Hilliard L, Woods G, Patel K, Goldenberg N, Lowe E, Jaffray J, Young G, Rajpurkar M, Davila J, Mahajerin A, Cooper J, Gunawardena S, Zia A, Journeycake J, Carpenter S, Guerrera M, Diab Y, Tarango C, Gruppo R, Acharya S, Torres M, Shaffer L, Mignacca R, Haley K, Recht M, Thornburg C, Shah N, Mullen C, Mitchell D, Nakar C, Betensky M, Lawrence C, Takemoto C, Lo C, Scott-Emuakpor A, Kulkarni R, Borst A, O'Brien S, Corales-Medina F, Narang S, Kucine N, Wang M, Panigrahi A, McGowan K, Cramer S, Dandekar S, Xavier F, Knoll K, Verma A, Geddes A, Ahuja S, Hege K, Raybagkar D, Sharathkumar A, Srivath L, Khan O, Druzgal C, Bhatt M, Chan A, Brandao L, Massicotte P, van Ommen C, Male C, Monagle P, Nakano T, Mitchell W, Hiatt W, Weitz J. Effect of Anticoagulant Therapy for 6 Weeks vs 3 Months on Recurrence and Bleeding Events in Patients Younger Than 21 Years of Age With Provoked Venous Thromboembolism. JAMA: The Journal Of The American Medical Association 2022, 327: 129-137. PMID: 35015038, PMCID: PMC8753509, DOI: 10.1001/jama.2021.23182.
- Roberts J, Recht M, Gonzales S, Stanley J, Denne M, Caicedo J, Rockwood K. Incorporating the patient voice and patient engagement in GOAL‐Hēm: Advancing patient‐centric hemophilia care. Research And Practice In Thrombosis And Haemostasis 2022, 6: e12655. PMID: 35155975, PMCID: PMC8822263, DOI: 10.1002/rth2.12655.
- Buckner T, Daoud N, Miles M, O'Neill C, Watson C, Recht M. Designing ATHN 7: Safety, effectiveness and practice of treatment of people with haemophilia in the United States through a natural history cohort study. The Journal Of Haemophilia Practice 2022, 9: 147-155. DOI: 10.2478/jhp-2022-0020.
- Eyster M, Sullivan S, MacDougall A, Jaworski K, Noble R, Curran M, Kuranda K, Chang T, Reape K, George L, Monahan P, Ragni M, Croteau S, Rasko J, Recht M, Samelson-Jones B, Mingozzi F, Anguela X, High K. Multiyear Factor VIII Expression after AAV Gene Transfer for Hemophilia A. The New England Journal Of Medicine 2021, 385: 1961-1973. PMID: 34788507, PMCID: PMC8672712, DOI: 10.1056/nejmoa2104205.
- He C, Hinds D, Pezalla E, Cheng D, Chen E, Sammon J, Solari P, Recht M. Health insurance coverage and switching among people with hemophilia A in the United States. Journal Of Managed Care & Specialty Pharmacy 2021, 28: 232-243. PMID: 34780299, PMCID: PMC12128936, DOI: 10.18553/jmcp.2021.21311.
- Valentino L, Baker J, Butler R, Escobar M, Frick N, Karp S, Koulianos K, Lattimore S, Nugent D, Pugliese J, Recht M, Reding M, Rice M, Thibodeaux C, Skinner M. Integrated Hemophilia Patient Care via a National Network of Care Centers in the United States: A Model for Rare Coagulation Disorders. Journal Of Blood Medicine 2021, 12: 897-911. PMID: 34707421, PMCID: PMC8544265, DOI: 10.2147/jbm.s325031.
- Veeranki S, Pednekar P, Graf M, Tuly R, Recht M, Batt K. A Delphi Consensus Approach for Difficult-to-Treat Patients with Severe Hemophilia A without Inhibitors. Journal Of Blood Medicine 2021, 12: 913-928. PMID: 34707422, PMCID: PMC8544791, DOI: 10.2147/jbm.s334852.
- Konkle B, Quon D, Raffini L, Recht M, Radulescu V, Carpenter S, Dunn A, Lu M, Watt M. A Prospective Observational Study of Antihemophilic Factor (Recombinant) Prophylaxis Related to Physical Activity Levels in Patients with Hemophilia A in the United States (SPACE). Journal Of Blood Medicine 2021, 12: 883-896. PMID: 34703348, PMCID: PMC8523903, DOI: 10.2147/jbm.s327180.
- Escobar M, Castaman G, Boix S, Callaghan M, de Moerloose P, Ducore J, Hermans C, Journeycake J, Leissinger C, Luck J, Mahlangu J, Miesbach W, Mitha I, Négrier C, Quon D, Recht M, Schved J, Shapiro A, Sidonio R, Srivastava A, Stasyshyn O, Vilchevska K, Wang M, Young G, Alexander W, Al‐Sabbagh A, Bonzo D, Macie C, Wilkinson T, Kessler C. The safety of activated eptacog beta in the management of bleeding episodes and perioperative haemostasis in adult and paediatric haemophilia patients with inhibitors. Haemophilia 2021, 27: 921-931. PMID: 34636112, PMCID: PMC9292935, DOI: 10.1111/hae.14419.
- Garrison L, Pezalla E, Towse A, Yang H, Faust E, Wu E, Li N, Sawyer E, Recht M. Hemophilia Gene Therapy Value Assessment: Methodological Challenges and Recommendations. Value In Health 2021, 24: 1628-1633. PMID: 34711363, DOI: 10.1016/j.jval.2021.05.008.
- Witkop M, Morgan G, O'Hara J, Recht M, Buckner T, Nugent D, Curtis R, O'Mahony B, Skinner M, Mulhern B, Cawson M, Ali T, Sawyer E, Li N. Patient preferences and priorities for haemophilia gene therapy in the US: A discrete choice experiment. Haemophilia 2021, 27: 769-782. PMID: 34310811, PMCID: PMC9290457, DOI: 10.1111/hae.14383.
- Nolan B, Klukowska A, Shapiro A, Rauch A, Recht M, Ragni M, Curtin J, Gunawardena S, Mukhopadhyay S, Jayawardene D, Winding B, Fischer K, Liesner R. Final results of the PUPs B-LONG study: evaluating safety and efficacy of rFIXFc in previously untreated patients with hemophilia B. Blood Advances 2021, 5: 2732-2739. PMID: 34242387, PMCID: PMC8288672, DOI: 10.1182/bloodadvances.2020004085.
- Sampson M, Cheng D, Recht M, Fargo J. The effect of age at diagnosis of type 1 von Willebrand disease on diagnostic laboratory values: A paediatric perspective. Haemophilia 2021, 27: e412-e414. PMID: 33533138, DOI: 10.1111/hae.14265.
- Recht M. Safety first: Tracking adverse events associated with new therapies for people with hemophilia. Journal Of Thrombosis And Haemostasis 2021, 19: 3-5. PMID: 33331044, DOI: 10.1111/jth.15188.
- Witkop M, Wang M, Hernandez G, Recht M, Baumann K, Cooper D. Impact of haemophilia on patients with mild‐to‐moderate disease: Results from the P‐FiQ and B‐HERO‐S studies. Haemophilia 2021, 27: 8-16. PMID: 33522654, DOI: 10.1111/hae.14251.
- Li N, Sawyer E, Maruszczyk K, Guzauskas G, Slomka M, Burke T, Martin A, O’Hara J, Stevenson M, Recht M. Adult lifetime cost of hemophilia B management in the US: payer and societal perspectives from a decision analytic model. Journal Of Medical Economics 2021, 24: 363-372. PMID: 33591884, DOI: 10.1080/13696998.2021.1891088.
- Reipert B, Gangadharan B, Hofbauer C, Berg V, Schweiger H, Bowen J, Blatny J, Fijnvandraat K, Mullins E, Klintman J, Male C, McGuinn C, Meeks S, Radulescu V, Ragni M, Recht M, Shapiro A, Staber J, Yaish H, Santagostino E, Brown D. The prospective Hemophilia Inhibitor PUP Study reveals distinct antibody signatures prior to FVIII inhibitor development. Blood Advances 2020, 4: 5785-5796. PMID: 33232473, PMCID: PMC7686884, DOI: 10.1182/bloodadvances.2020002731.
- Lim M, Cheng D, Recht M, Kempton C, Key N. Management of inhibitors in persons with non‐severe hemophilia A in the United States. American Journal Of Hematology 2020, 96: e9-e11. PMID: 32976635, DOI: 10.1002/ajh.26011.
- Lim M, Cheng D, Recht M, Kempton C, Key N. Inhibitors and mortality in persons with nonsevere hemophilia A in the United States. Blood Advances 2020, 4: 4739-4747. PMID: 33007074, PMCID: PMC7556148, DOI: 10.1182/bloodadvances.2020002626.
- Goldscheitter G, Recht M, Sochacki P, Manco‐Johnson M, Taylor J. Biomarkers of bone disease in persons with haemophilia. Haemophilia 2020, 27: 149-155. PMID: 32856388, DOI: 10.1111/hae.13986.
- Ahuja S, Recht M, Konkle B. Hemostatic Therapies for Heavy Menstrual Bleeding. 2020, 119-127. DOI: 10.1007/978-3-030-48446-0_11.
- Malec L, Cheng D, Witmer C, Jaffray J, Kouides P, Haley K, Sidonio R, Johnson K, Recht M, White G, Croteau S, Ragni M. The impact of extended half‐life factor concentrates on prophylaxis for severe hemophilia in the United States. American Journal Of Hematology 2020, 95: 960-965. PMID: 32356313, DOI: 10.1002/ajh.25844.
- Wang M, Recht M, Iyer N, Cooper D, Soucie J. Hemophilia without prophylaxis: Assessment of joint range of motion and factor activity. Research And Practice In Thrombosis And Haemostasis 2020, 4: e12347. PMID: 32864554, PMCID: PMC7443428, DOI: 10.1002/rth2.12347.
- Marshall A, Recht M, Sridharan M, Nichols W, Ashrani A, Fischer K, Miles M, Riedel A, Pruthi R. A study of dedicated haemophilia carrier clinics in the United States: Prevalence, services offered and barriers to development. Haemophilia 2020, 26: e253-e255. PMID: 32537802, DOI: 10.1111/hae.14071.
- Konkle B, Recht M, Hilger A, Marks P. The critical need for postmarketing surveillance in gene therapy for haemophilia. Haemophilia 2020, 27: 126-131. PMID: 32495492, DOI: 10.1111/hae.13972.
- Warren B, Thornhill D, Stein J, Fadell M, Ingram J, Funk S, Norton K, Lane H, Bennett C, Dunn A, Recht M, Shapiro A, Manco-Johnson M. Young adult outcomes of childhood prophylaxis for severe hemophilia A: results of the Joint Outcome Continuation Study. Blood Advances 2020, 4: 2451-2459. PMID: 32492157, PMCID: PMC7284094, DOI: 10.1182/bloodadvances.2019001311.
- Buckner T, Watson C, Recht M. Emicizumab in Hemophilia A. The New England Journal Of Medicine 2020, 382: 785-786. PMID: 32074441, DOI: 10.1056/nejmc1916299.
- Haley K, Sidonio R, Abraham S, Cheng D, Recht M, Kulkarni R. A Cross-Sectional Study of Women and Girls with Congenital Bleeding Disorders: The American Thrombosis and Hemostasis Network Cohort. Journal Of Women's Health 2020, 29: 670-676. PMID: 31905045, DOI: 10.1089/jwh.2019.7930.
- Von Drygalski A, Giermasz A, Castaman G, Key N, Lattimore S, Leebeek F, Miesbach W, Recht M, Long A, Gut R, Sawyer E, Pipe S. Etranacogene dezaparvovec (AMT-061 phase 2b): normal/near normal FIX activity and bleed cessation in hemophilia B. Blood Advances 2019, 3: 3241-3247. PMID: 31698454, PMCID: PMC6855101, DOI: 10.1182/bloodadvances.2019000811.
- Konkle B, Recht M, Group T. The national blueprint for 21st century data and specimen collection and observational cohort studies: NHLBI State of the Science Workshop on factor VIII inhibitors. Haemophilia 2019, 25: 590-594. PMID: 31329362, DOI: 10.1111/hae.13772.
- Warren B, Jacobson L, Kempton C, Buchanan G, Recht M, Brown D, Leissinger C, Shapiro A, Abshire T, Manco-Johnson M, Manco-Johnson M, Abshire T, Shapiro A, Riske B, Hacker M, Kilcoyne R, Ingram J, Manco-Johnson M, Funk S, Jacobson L, Valentino L, Hoots W, Buchanan G, DiMichele D, Recht M, Brown D, Leissinger C, Bleak S, Cohen A, Mathew P, Matsunaga A, Medeiros D, Nugent D, Thomas G, Thompson A, McRedmond K, Soucie J, Austin H, Evatt B. Factor VIII prophylaxis effects outweigh other hemostasis contributors in predicting severe haemophilia A joint outcomes. Haemophilia 2019, 25: 867-875. PMID: 31115111, PMCID: PMC7273872, DOI: 10.1111/hae.13778.
- Yu J, Iorio A, Edginton A, co‐investigators O, Ahuja S, Román M, Arrieta M, Arola M, Barillari G, Balasa V, Belletrutti M, Moreno R, Beurrier P, Bidlingmaier C, Blanchette V, Blatny J, Bonanad S, Brose K, Brown D, Byant P, Canaro M, Carvalho M, Catarino C, Chitlur M, Cockrell E, Chowdary P, Cnossen M, Collins P, Coppens M, Croteau S, Cultrera D, de Cristofaro R, de Raucourt E, Desprez D, Dunn A, El‐Ekiabi M, Kotnik B, Fischer K, Frotscher B, Garbiero S, Ruiz R, Gill J, del Castillo C, Gottstein S, Lassandro G, Giordano P, Hart D, Hegemann I, Hermans C, Hua B, Hwang N, Jackson S, James P, Katsarou O, Kavakli K, Kempton C, Kentouche K, Khan O, Kobelt R, Kruse‐Jarres R, Laane E, Larson E, Lassila R, Lee A, Poon M, Lissick J, Langstrom S, Mahlangu J, Makris M, Marchesini E, Mateo J, Vera P, Martorell M, Matsushita T, McCrae S, Mignot‐Castellano E, Montcrieff C, Maes P, Mondelars V, Bekart M, Mora E, Morales J, Mourey G, Bertrand M, Napolitano M, Siragusa S, Negrier C, Neme D, Niinimaki R, Oldenburg J, Albert T, Ornstein D, Ozelo M, Panetta J, Neufeld E, P'Ng S, Peerlinck K, Pollio B, Pouplard C, Gruel Y, Prezotti A, Price V, Primacakti F, Puyade M, Radossi P, Raffini L, Ragni M, Rangarajan S, Reding M, Reid R, Restrepo J, Ramirez J, Recht M, Lopez M, Ruiz‐Sàez A, Saleh M, Shapiro A, Sharathkumar A, Selmeczi A, Simpson M, Singleton T, Cruz M, Soto V, Steele M, Streif W, Sun H, Ritchie B, Sun J, Feng X, Suzuki T, Nagao A, Takemoto C, Tapp H, Teitel J, Tinmouth A, Thornburg C, Tosseto A, Turnstall O, Vezina C, Warren B, Wheeler A, Gutierrez J, Wu J, Wynn T, Yang R, Young G, Zanon E, Zupan I. Using pharmacokinetics for tailoring prophylaxis in people with hemophilia switching between clotting factor products: A scoping review. Research And Practice In Thrombosis And Haemostasis 2019, 3: e12204. PMID: 31294337, PMCID: PMC6611373, DOI: 10.1002/rth2.12204.
- Mahlangu J, Oldenburg J, Callaghan M, Shima M, Mancuso M, Trask P, Recht M, Garcia C, Yang R, Lehle M, Macharia H, Asikanius E, Levy G, Kruse‐Jarres R, von Mackensen S. Health‐related quality of life and health status in persons with haemophilia A with inhibitors: A prospective, multicentre, non‐interventional study (NIS). Haemophilia 2019, 25: 382-391. PMID: 31016855, PMCID: PMC6850115, DOI: 10.1111/hae.13731.
- Aledort L, Carpenter S, Cuker A, Kulkarni R, Recht M, Young G, Leissinger C. Why plasma‐derived factor VIII? Haemophilia 2019, 25: e183-e185. PMID: 30866124, DOI: 10.1111/hae.13705.
- Samuelson Bannow B, Recht M, Négrier C, Hermans C, Berntorp E, Eichler H, Mancuso M, Klamroth R, O'Hara J, Santagostino E, Matsushita T, Kessler C. Factor VIII: Long-established role in haemophilia A and emerging evidence beyond haemostasis. Blood Reviews 2019, 35: 43-50. PMID: 30922616, DOI: 10.1016/j.blre.2019.03.002.
- Winsnes K, Sochacki P, Eriksson C, Shereck E, Recht M, Johnson K, De Mola R, Stork L. Delirium in the pediatric hematology, oncology, and bone marrow transplant population. Pediatric Blood & Cancer 2019, 66: e27640. PMID: 30697919, DOI: 10.1002/pbc.27640.
- Mahlangu J, Oldenburg J, Callaghan M, Shima M, Santagostino E, Moore M, Recht M, Garcia C, Yang R, Lehle M, Macharia H, Asikanius E, Levy G, Kruse‐Jarres R. Bleeding events and safety outcomes in persons with haemophilia A with inhibitors: A prospective, multi‐centre, non‐interventional study. Haemophilia 2018, 24: 921-929. PMID: 30295389, DOI: 10.1111/hae.13612.
- Gruppo R, Malan D, Kapocsi J, Nemes L, Hay C, Boggio L, Chowdary P, Tagariello G, von Drygalski A, Hua F, Scaramozza M, Arkin S, Investigators F, Hermans C, Claes C, Hanes I, Huyghe I, Kantaridis C, da Costa L, Ndongo M, Petit W, Santagostino E, Cannavo A, Fasulo M, Mancuso M, Tosetto A, Castaman G, Candiotto L, Radossi P, Scarpa E, Smith M, Dick A, Robson R, Waaka D, Wynne C, Punt Z, Kavakli K, Balkan C, Duyu M, Goksel S, Karapinar B, Ozyurek A, Saydam G, Karapinar D, Laffan M, Millar C, Suppiah P, Rizleigh C, Chowdary G, Davies J, Fosbury E, Gill S, Pike G, Thachil J, Recht M, Deutsche J, Taylor J, Kalinyak K, Mullins E, Palumbo J, Quinn C, Tarango C, Tarabar S, Chandler P, Deats L, Deshpande S, Epstein N, Hansson A, Pawlak S, Rudin D, Valentino L, Kakodkar N, Simpson M, Fogarty P, Bach T, Chiang E, Adamson J, Glass C, Sidhu N, Tucker‐Greene T. Phase 1, single‐dose escalating study of marzeptacog alfa (activated), a recombinant factor VIIa variant, in patients with severe hemophilia. Journal Of Thrombosis And Haemostasis 2018, 16: 1984-1993. PMID: 30151972, DOI: 10.1111/jth.14247.
- Croteau S, Callaghan M, Davis J, Dunn A, Guerrera M, Khan O, Neufeld E, Raffini L, Recht M, Wang M, Iorio A. Focusing in on use of pharmacokinetic profiles in routine hemophilia care. Research And Practice In Thrombosis And Haemostasis 2018, 2: e12118. PMID: 30046766, PMCID: PMC6046597, DOI: 10.1002/rth2.12118.
- Manco‐Johnson M, Byams V, Recht M, Dudley B, Dupervil B, Aschman D, Oakley M, Kapica S, Voutsis M, Humes S, Kulkarni R, Grant A, Network. O. Community counts: Evolution of a national surveillance system for bleeding disorders. American Journal Of Hematology 2018, 93: e137-e140. PMID: 29473207, PMCID: PMC6145085, DOI: 10.1002/ajh.25076.
- Roberts J, Lattimore S, Recht M, Jackson S, Gue D, Squire S, Robinson K, Price V, Denne M, Richardson S, Rockwood K. Goal Attainment Scaling for haemophilia (GAS‐Hēm): testing the feasibility of a new patient‐centric outcome measure in people with haemophilia. Haemophilia 2018, 24: e199-e206. PMID: 29626387, DOI: 10.1111/hae.13454.
- Buckner T, Batt K, Quon D, Witkop M, Recht M, Kessler C, Baumann K, Hernandez G, Wang M, Cooper D, Kempton C. Assessments of pain, functional impairment, anxiety, and depression in US adults with hemophilia across patient‐reported outcome instruments in the Pain, Functional Impairment, and Quality of Life (P‐FiQ) study. European Journal Of Haematology 2018, 100: 5-13. PMID: 29498784, DOI: 10.1111/ejh.13027.
- Batt K, Boggio L, Neff A, Buckner T, Wang M, Quon D, Witkop M, Recht M, Kessler C, Iyer N, Cooper D. Patient‐reported outcomes and joint status across subgroups of US adults with hemophilia with varying characteristics: Results from the Pain, Functional Impairment, and Quality of Life (P‐FiQ) study. European Journal Of Haematology 2018, 100: 14-24. PMID: 29498783, DOI: 10.1111/ejh.13028.
- Rocheleau A, Khader A, Ngo A, Boehnlein C, McDavitt C, Lattimore S, Recht M, McCarty O, Haley K. Pilot study of novel lab methodology and testing of platelet function in adolescent women with heavy menstrual bleeding. Pediatric Research 2018, 83: 693-701. PMID: 29166373, PMCID: PMC5902421, DOI: 10.1038/pr.2017.298.
- Kempton C, Recht M, Neff A, Wang M, Buckner T, Soni A, Quon D, Witkop M, Boggio L, Gut R, Cooper D. Impact of pain and functional impairment in US adults with haemophilia: Patient‐reported outcomes and musculoskeletal evaluation in the pain, functional impairment and quality of life (P‐FiQ) study. Haemophilia 2017, 24: 261-270. PMID: 29218759, DOI: 10.1111/hae.13377.
- Kempton C, Wang M, Recht M, Neff A, Shapiro A, Soni A, Kulkarni R, Buckner T, Batt K, Iyer N, Cooper D. Reliability of patient-reported outcome instruments in US adults with hemophilia: the Pain, Functional Impairment and Quality of life (P-FiQ) study. Patient Preference And Adherence 2017, 11: 1603-1612. PMID: 29033549, PMCID: PMC5614789, DOI: 10.2147/ppa.s141389.
- Batt K, Recht M, Cooper D, Iyer N, Kempton C. Construct validity of patient-reported outcome instruments in US adults with hemophilia: results from the Pain, Functional Impairment, and Quality of life (P-FiQ) study. Patient Preference And Adherence 2017, 11: 1369-1380. PMID: 28860720, PMCID: PMC5558590, DOI: 10.2147/ppa.s141390.
- Ullman M, Zhang Q, Grosse S, Recht M, Soucie J, Investigators T. Prophylaxis use among males with haemophilia B in the United States. Haemophilia 2017, 23: 910-917. PMID: 28780772, PMCID: PMC5724962, DOI: 10.1111/hae.13317.
- Shatzel J, Azar S, Scherber R, Gay N, Deloughery T, VanSandt A, Kruse‐Jarres R, Recht M, Taylor J. Unexpected pharmacokinetics of recombinant porcine factor VIII in a patient with acquired factor VIII deficiency and spontaneous epidural haematoma. Haemophilia 2017, 23: e453-e456. PMID: 28664642, DOI: 10.1111/hae.13247.
- Kahan S, Cuker A, Kushner R, Maahs J, Recht M, Wadden T, Willis T, Majumdar S, Ungar D, Cooper D. Prevalence and impact of obesity in people with haemophilia: Review of literature and expert discussion around implementing weight management guidelines. Haemophilia 2017, 23: 812-820. PMID: 28636076, DOI: 10.1111/hae.13291.
- Recht M, Rajpurkar M, Chitlur M, d'Oiron R, Zotz R, Di Minno G, Cooper D, Poon M. Independent adjudicator assessments of platelet refractoriness and rFVIIa efficacy in bleeding episodes and surgeries from the multinational Glanzmann's thrombasthenia registry. American Journal Of Hematology 2017, 92: 646-652. PMID: 28370369, DOI: 10.1002/ajh.24741.
- Witkop M, Neff A, Buckner T, Wang M, Batt K, Kessler C, Quon D, Boggio L, Recht M, Baumann K, Gut R, Cooper D, Kempton C. Self‐reported prevalence, description and management of pain in adults with haemophilia: methods, demographics and results from the Pain, Functional Impairment, and Quality of life (P‐FiQ) study. Haemophilia 2017, 23: 556-565. PMID: 28419637, DOI: 10.1111/hae.13214.
- Chitlur M, Rajpurkar M, Recht M, Tarantino M, Yee D, Cooper D, Gunawardena S. Recognition and management of platelet-refractory bleeding in patients with Glanzmann’s thrombasthenia and other severe platelet function disorders. International Journal Of General Medicine 2017, 10: 95-99. PMID: 28435309, PMCID: PMC5388206, DOI: 10.2147/ijgm.s128953.
- Buckner T, Witkop M, Guelcher C, Frey M, Hunter S, Peltier S, Recht M, Walsh C, Kessler C, Owens W, Clark D, Frick N, Rice M, Iyer N, Holot N, Cooper D, Sidonio R. Management of US men, women, and children with hemophilia and methods and demographics of the Bridging Hemophilia B Experiences, Results and Opportunities into Solutions (B‐HERO‐S) study. European Journal Of Haematology 2017, 98: 5-17. PMID: 28319338, DOI: 10.1111/ejh.12854.
- Oleson D, Fox L, Nguyen T, Sochacki P, McCarthy M, Adams E, Recht M. A comparison of two types of ankle supports in men with haemophilia and unilateral ankle pain from arthropathy. Haemophilia 2017, 23: 444-448. PMID: 28220573, DOI: 10.1111/hae.13184.
- Recht M, Chitlur M, Lam D, Sarnaik S, Rajpurkar M, Cooper D, Gunawardena S. Epistaxis as a Common Presenting Symptom of Glanzmann’s Thrombasthenia, a Rare Qualitative Platelet Disorder: Illustrative Case Examples. Case Reports In Emergency Medicine 2017, 2017: 8796425. PMID: 28299211, PMCID: PMC5337314, DOI: 10.1155/2017/8796425.
- Aledort L, Recht M, Kulkarni R, Kobrinsky N. Adult, previously untreated patients remain a significant therapeutic challenge. Journal Of Thrombosis And Haemostasis 2016, 14: 2075-2076. PMID: 27496600, DOI: 10.1111/jth.13434.
- Recht M, Konkle B, Jackson S, Neufeld E, Rockwood K, Pipe S. Recognizing the need for personalization of haemophilia patient‐reported outcomes in the prophylaxis era. Haemophilia 2016, 22: 825-832. PMID: 27581872, DOI: 10.1111/hae.13066.
- Lentz S, Cerqueira M, Janic D, Kempton C, Matytsina I, Misgav M, Oldenburg J, Ozelo M, Recht M, Rosholm A, Savic A, Suzuki T, Tiede A, Santagostino E. Interim results from a large multinational extension trial (guardian™2) using turoctocog alfa for prophylaxis and treatment of bleeding in patients with severe haemophilia A. Haemophilia 2016, 22: e445-e449. PMID: 27291066, DOI: 10.1111/hae.12990.
- Baker‐Groberg S, Lattimore S, Recht M, McCarty O, Haley K. Assessment of neonatal platelet adhesion, activation, and aggregation. Journal Of Thrombosis And Haemostasis 2016, 14: 815-827. PMID: 26806373, PMCID: PMC4828266, DOI: 10.1111/jth.13270.
- Mahlangu J, Weldingh K, Lentz S, Kaicker S, Karim F, Matsushita T, Recht M, Tomczak W, Windyga J, Ehrenforth S, Knobe K, Investigators F, Weltermann A, de Paula E, Cerqueira M, Zupancic‐Salek S, Katsarou O, Economou M, Nemes L, Boda Z, Santagostino E, Tagariello G, Hanabusa H, Fukutake K, Shima M, Serban M, Elezovic I, Savic A, Shen M, Chuansumrit A, Angchaisuksiri P, Kavakli K, Sasmaz I, Madan B, Giangrande P, Kempton C, Young G, Quon D, Ameri A, Kuriakose P, Obzut D, Wang M, Ortiz I. Changes in the amino acid sequence of the recombinant human factor VIIa analog, vatreptacog alfa, are associated with clinical immunogenicity. Journal Of Thrombosis And Haemostasis 2015, 13: 1989-1998. PMID: 26362483, DOI: 10.1111/jth.13141.
- Goldenberg N, Abshire T, Blatchford P, Fenton L, Halperin J, Hiatt W, Kessler C, Kittelson J, Manco‐Johnson M, Spyropoulos A, Steg P, Stence N, Turpie A, Schulman S, Punzalan R, Wang M, Jaffray J, Young G, Rajpurkar M, Carpenter S, Diab Y, Verdun N, Tarango C, Acharya S, Torres M, Kucine N, Mitchell B, Shah N, Thornburg C, Takemoto C, Kulkarni R, O'Brien S, Haley K, Recht M, Knoll C, Thornburg C, Geddis A, Ahuja S, Simpson M, Srivaths L, Journeycake J, Zia A. Multicenter randomized controlled trial on Duration of Therapy for Thrombosis in Children and Young Adults (the Kids‐DOTT trial): pilot/feasibility phase findings. Journal Of Thrombosis And Haemostasis 2015, 13: 1597-1605. PMID: 26118944, PMCID: PMC4561031, DOI: 10.1111/jth.13038.
- Gay N, Lee S, Liel M, Sochacki P, Recht M, Taylor J. Increased fracture rates in people with haemophilia: a 10‐year single institution retrospective analysis. British Journal Of Haematology 2015, 170: 584-586. PMID: 25659575, DOI: 10.1111/bjh.13312.
- Nathwani A, Reiss U, Tuddenham E, Rosales C, Chowdary P, McIntosh J, Della Peruta M, Lheriteau E, Patel N, Raj D, Riddell A, Pie J, Rangarajan S, Bevan D, Recht M, Shen Y, Halka K, Basner-Tschakarjan E, Mingozzi F, High K, Allay J, Kay M, Ng C, Zhou J, Cancio M, Morton C, Gray J, Srivastava D, Nienhuis A, Davidoff A. Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B. The New England Journal Of Medicine 2014, 371: 1994-2004. PMID: 25409372, PMCID: PMC4278802, DOI: 10.1056/nejmoa1407309.
- Maahs J, Donkin J, Recht M, Cooper D. Mixing and administration times of bypassing agents: observations from the Dosing Observational Study in Hemophilia (DOSE). Journal Of Blood Medicine 2014, 5: 153-156. PMID: 25187744, PMCID: PMC4149444, DOI: 10.2147/jbm.s61859.
- Recht M, Neufeld E, Sharma V, Solem C, Pickard A, Gut R, Cooper D. Impact of Acute Bleeding on Daily Activities of Patients with Congenital Hemophilia with Inhibitors and Their Caregivers and Families: Observations from the Dosing Observational Study in Hemophilia (DOSE). Value In Health 2014, 17: 744-748. PMID: 25236999, DOI: 10.1016/j.jval.2014.07.003.
- Rajpurkar M, Chitlur M, Recht M, Cooper D. Use of recombinant activated factor VII in patients with Glanzmann's thrombasthenia: a review of the literature. Haemophilia 2014, 20: 464-471. PMID: 24948404, DOI: 10.1111/hae.12473.
- Haley K, Recht M, McCarty O. Neonatal platelets: mediators of primary hemostasis in the developing hemostatic system. Pediatric Research 2014, 76: 230-237. PMID: 24941213, PMCID: PMC4348010, DOI: 10.1038/pr.2014.87.
- Haley K, Russell T, Boshkov L, Leger R, Garratty G, Recht M, Nazemi K. Fatal carboplatin-induced immune hemolytic anemia in a child with a brain tumor. Journal Of Blood Medicine 2014, 5: 55-58. PMID: 24868179, PMCID: PMC4031206, DOI: 10.2147/jbm.s59192.
- Adams E, Deutsche J, Okoroh E, Owens‐McAlister S, Majumdar S, Ullman M, Damiano M, Recht M, Group T. An inventory of healthy weight practices in federally funded haemophilia treatment centres in the United States. Haemophilia 2014, 20: 639-643. PMID: 24629074, PMCID: PMC4484574, DOI: 10.1111/hae.12385.
- Recht M, Liel M, Turner R, Klein R, Taylor J. The bone disease associated with factor VIII deficiency in mice is secondary to increased bone resorption. Haemophilia 2013, 19: 908-912. PMID: 23731369, DOI: 10.1111/hae.12195.
- Soucie J, Monahan P, Kulkarni R, De Staercke C, Recht M, Chitlur M, Gruppo R, Hooper W, Kessler C, Manco‐Johnson M, Powell J, Pyle M, Riske B, Sabio H, Trimble S. Evidence for the continued transmission of parvovirus B19 in patients with bleeding disorders treated with plasma‐derived factor concentrates. Transfusion 2013, 53: 1143-1144. PMID: 23659532, DOI: 10.1111/trf.12153.
- Lentz S, Misgav M, Ozelo M, Šalek S, Veljkovic D, Recht M, Cerqueira M, Tiede A, Brand B, Mancuso M, Seremetis S, Lindblom A, Martinowitz U. Results from a large multinational clinical trial (guardian™1) using prophylactic treatment with turoctocog alfa in adolescent and adult patients with severe haemophilia A: safety and efficacy. Haemophilia 2013, 19: 691-697. PMID: 23647704, DOI: 10.1111/hae.12159.
- Lane J, McLaren P, Dorrell L, Shianna K, Stemke A, Pelak K, Moore S, Oldenburg J, Alvarez-Roman M, Angelillo-Scherrer A, Boehlen F, Bolton-Maggs P, Brand B, Brown D, Chiang E, Cid-Haro A, Clotet B, Collins P, Colombo S, Dalmau J, Fogarty P, Giangrande P, Gringeri A, Iyer R, Katsarou O, Kempton C, Kuriakose P, Lin J, Makris M, Manco-Johnson M, Tsakiris D, Martinez-Picado J, Mauser-Bunschoten E, Neff A, Oka S, Oyesiku L, Parra R, Peter-Salonen K, Powell J, Recht M, Shapiro A, Stine K, Talks K, Telenti A, Wilde J, Yee T, Wolinsky S, Martinson J, Hussain S, Bream J, Jacobson L, Carrington M, Goedert J, Haynes B, McMichael A, Goldstein D, Fellay J, Immunology F. A genome-wide association study of resistance to HIV infection in highly exposed uninfected individuals with hemophilia A. Human Molecular Genetics 2013, 22: 1903-1910. PMID: 23372042, PMCID: PMC3613165, DOI: 10.1093/hmg/ddt033.
- Soucie J, De Staercke C, Monahan P, Recht M, Chitlur M, Gruppo R, Hooper W, Kessler C, Kulkarni R, Manco‐Johnson M, Powell J, Pyle M, Riske B, Sabio H, Trimble S, Network H. Evidence for the transmission of parvovirus B19 in patients with bleeding disorders treated with plasma‐derived factor concentrates in the era of nucleic acid test screening. Transfusion 2012, 53: 1217-1225. PMID: 22998193, PMCID: PMC4519820, DOI: 10.1111/j.1537-2995.2012.03907.x.
- Neufeld E, Recht M, Sabio H, Saxena K, Solem C, Pickard A, Gut R, Cooper D. Effect of Acute Bleeding on Daily Quality of Life Assessments in Patients with Congenital Hemophilia with Inhibitors and Their Families: Observations from the Dosing Observational Study in Hemophilia. Value In Health 2012, 15: 916-925. PMID: 22999142, DOI: 10.1016/j.jval.2012.05.005.
- Auerswald G, Thompson A, Recht M, Brown D, Liesner R, Guzmán-Becerra N, Dyck-Jones J, Ewenstein B, Abbuehl B. Experience of Advate rAHF-PFM in previously untreated patients and minimally treated patients with haemophilia A. Thrombosis And Haemostasis 2012, 107: 1072-1082. PMID: 22476554, PMCID: PMC6292131, DOI: 10.1160/th11-09-0642.
- Liel M, Greenberg D, Recht M, Vanek C, Klein R, Taylor J. Decreased bone density and bone strength in a mouse model of severe factor VIII deficiency. British Journal Of Haematology 2012, 158: 140-143. PMID: 22469061, DOI: 10.1111/j.1365-2141.2012.09101.x.
- Chiu Y, Drolet B, Blei F, Carcao M, Fangusaro J, Kelly M, Krol A, Lofgren S, Mancini A, Metry D, Recht M, Silverman R, Tom W, Pope E. Variable response to propranolol treatment of kaposiform hemangioendothelioma, tufted angioma, and Kasabach–Merritt phenomenon. Pediatric Blood & Cancer 2012, 59: 934-938. PMID: 22648868, PMCID: PMC3528889, DOI: 10.1002/pbc.24103.
- Bradeen H, Shehab S, Recht M. Iron Metabolism and Iron Deficiency Anemia. 2012, 2963-2968. DOI: 10.1007/978-3-642-02202-9_318.
- Flood V, Recht M. Autoimmune Hemolytic Anemia. 2012, 2969-2974. DOI: 10.1007/978-3-642-02202-9_319.
- Richard N, Haley K, Recht M. Thalassemia. 2012, 3029-3036. DOI: 10.1007/978-3-642-02202-9_326.
- Wong T, Majumdar S, Adams E, Bergman S, Damiano M, Deutsche J, Recht M, Group H. Overweight and Obesity in Hemophilia A Systematic Review of the Literature. American Journal Of Preventive Medicine 2011, 41: s369-s375. PMID: 22099360, DOI: 10.1016/j.amepre.2011.09.008.
- Grace R, Bennett C, Ritchey A, Jeng M, Thornburg C, Lambert M, Neier M, Recht M, Kumar M, Blanchette V, Klaassen R, Buchanan G, Kurth M, Nugent D, Thompson A, Stine K, Kalish L, Neufeld E. Response to steroids predicts response to rituximab in pediatric chronic immune thrombocytopenia. Pediatric Blood & Cancer 2011, 58: 221-225. PMID: 21674758, PMCID: PMC3863944, DOI: 10.1002/pbc.23130.
- RECHT M, POLLMANN H, TAGLIAFERRI A, MUSSO R, JANCO R, NEUMAN W. A retrospective study to describe the incidence of moderate to severe allergic reactions to factor IX in subjects with haemophilia B. Haemophilia 2011, 17: 494-499. PMID: 21518148, DOI: 10.1111/j.1365-2516.2011.02436.x.
- SOUCIE J, WANG C, SIDDIQI A, KULKARNI R, RECHT M, KONKLE B, NETWORK T. The longitudinal effect of body adiposity on joint mobility in young males with Haemophilia A. Haemophilia 2011, 17: 196-203. PMID: 21332880, DOI: 10.1111/j.1365-2516.2010.02400.x.
- Wong T, Recht M. Current Options and New Developments in the Treatment of Haemophilia. Drugs 2011, 71: 305-320. PMID: 21319868, DOI: 10.2165/11585340-000000000-00000.
- Recht M. Thrombocytopenia and Anemia in Infants and Children. Emergency Medicine Clinics Of North America 2009, 27: 505-523. PMID: 19646651, DOI: 10.1016/j.emc.2009.04.009.
- RECHT M, NEMES L, MATYSIAK M, MANCO‐JOHNSON M, LUSHER J, SMITH M, MANNUCCI P, HAY C, ABSHIRE T, O’BRIEN A, HAYWARD B, UDATA C, ROTH D, ARKIN S. Clinical evaluation of moroctocog alfa (AF‐CC), a new generation of B‐domain deleted recombinant factor VIII (BDDrFVIII) for treatment of haemophilia A: demonstration of safety, efficacy, and pharmacokinetic equivalence to full‐length recombinant factor VIII. Haemophilia 2009, 15: 869-880. PMID: 19473411, DOI: 10.1111/j.1365-2516.2009.02027.x.
- SPENCER M, WODRICH D, SCHULTZ W, WAGNER L, RECHT M. Inattention, hyperactivity‐impulsivity, academic skills and psychopathology in boys with and without haemophilia. Haemophilia 2009, 15: 701-706. PMID: 19298375, DOI: 10.1111/j.1365-2516.2009.01993.x.
- VALENTINO L, RECHT M, DIPAOLA J, SHAPIRO A, PIPE S, EWING N, URGO J, BULLOCK T, SIMMONS M, DEGUZMAN C. Experience with a third generation recombinant factor VIII concentrate (Advate®) for immune tolerance induction in patients with haemophilia A. Haemophilia 2009, 15: 718-726. PMID: 19298383, DOI: 10.1111/j.1365-2516.2008.01960.x.
- GERSTNER G, DAMIANO M, TOM A, WORMAN C, SCHULTZ W, RECHT M, STOPECK A. Prevalence and risk factors associated with decreased bone mineral density in patients with haemophilia. Haemophilia 2009, 15: 559-565. PMID: 19187193, DOI: 10.1111/j.1365-2516.2008.01963.x.
- Manco-Johnson M, Abshire T, Shapiro A, Riske B, Hacker M, Kilcoyne R, Ingram J, Manco-Johnson M, Funk S, Jacobson L, Valentino L, Hoots W, Buchanan G, DiMichele D, Recht M, Brown D, Leissinger C, Bleak S, Cohen A, Mathew P, Matsunaga A, Medeiros D, Nugent D, Thomas G, Thompson A, McRedmond K, Soucie J, Austin H, Evatt B. Prophylaxis versus Episodic Treatment to Prevent Joint Disease in Boys with Severe Hemophilia. The New England Journal Of Medicine 2007, 357: 535-544. PMID: 17687129, DOI: 10.1056/nejmoa067659.
- LAMBERT T, RECHT M, VALENTINO L, POWELL J, UDATA C, SULLIVAN S, ROTH D. Reformulated BeneFix®: efficacy and safety in previously treated patients with moderately severe to severe haemophilia B. Haemophilia 2007, 13: 233-243. PMID: 17498071, DOI: 10.1111/j.1365-2516.2007.01458.x.
- Hay C, Recht M, Carcao M, Reipert B. Current and Future Approaches to Inhibitor Management and Aversion. Seminars In Thrombosis And Hemostasis 2006, 32: 015-021. PMID: 16804831, DOI: 10.1055/s-2006-946910.
- Wodrich D, Recht M, Gradowski M, Wagner L. Is attention deficit hyperactivity disorder over‐represented among HIV‐seronegative boys with haemophilia? Preliminary results from our centre. Haemophilia 2003, 9: 593-597. PMID: 14511300, DOI: 10.1046/j.1365-2516.2003.00790.x.
- Rincón M, Enslen H, Raingeaud J, Recht M, Zapton T, Su M, Penix L, Davis R, Flavell R. Interferon‐γ expression by Th1 effector T cells mediated by the p38 MAP kinase signaling pathway. The EMBO Journal 1998, 17: 2817-2829. PMID: 9582275, PMCID: PMC1170622, DOI: 10.1093/emboj/17.10.2817.
- Rinder HM, Tracey JB, Recht M, DeCastro L, Rinder CS, McHugh C, Smith BR. Differences in Platelet α-granule Release between Normals and Immune Thrombocytopenic Patients and between Young and Old Platelets. Thrombosis And Haemostasis 1998, 80: 457-462. PMID: 9759627, DOI: 10.1055/s-0037-1615229.
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