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Clinical Trials
Michele Spencer-Manzon
Clinical Trials
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Disease Type
Brain, Spinal Cord & Nervous System
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Children's Health
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Brain, Spinal Cord & Nervous System, Genetics
A Study to Evaluate Efficacy and Safety of Vatiquinone for Treating Mitochondrial Disease in Participants With Refractory Epilepsy (MIT-E)
Ages
18 years and younger
Gender
Both
Children's Health, Genetics
Pediatric Genomics Discovery Program (PGDP)
Gender
Both
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