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AnnMarie Liapakis
Clinical Trials
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Disease Type
Brain, Spinal Cord & Nervous System
(1)
Genetics
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Genetics
Efficacy and Safety of WTX101 Administered for 48 Weeks Versus Standard of Care in Wilson Disease Subjects
Ages
12 years and older
Gender
Both
Date
04/02/2018
Brain, Spinal Cord & Nervous System, Vision/Eye, Liver
Wilson Disease Registry
Gender
Both
Date
11/16/2017
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